New Long-Term treatment aims to stop bleeds in haemophilia patients

NCT ID NCT05685238

Summary

This study is testing the long-term safety and effectiveness of a new medicine called Mim8 for people with haemophilia A. Mim8 is designed to prevent bleeding episodes by helping the blood to clot. The study will follow participants for up to 5.5 years to see how well the treatment works and monitor for any side effects.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • A.O.U. Città della Salute e della Scienza di Torino-Ospedale

    Torino, 10126, Italy

  • A.O.U. Policlinico Umberto I

    Rome, Lazio, 00161, Italy

  • A.O.U. Policlinico Umberto I

    Rome, 00161, Italy

  • AKH - Klin. Abt. f. Haematologie u. Haemostaseologie

    Vienna, 1090, Austria

  • AOU Careggi Firenze

    Florence, 50134, Italy

  • Acıbadem Adana Hastanesi-Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • Akdeniz Universitesi

    Antalya, 01010, Turkey (Türkiye)

  • Akdeniz Üniversitesi Hastanesi- Hematoloji

    Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)

  • AmsterdamUMC AMC

    Amsterdam, 1105 AZ, Netherlands

  • Ap-Hp-Hopital de Bicetre

    Le Kremlin-Bicêtre, 94275, France

  • Ap-Hp-Hopital de Bicetre-1

    Le Kremlin-Bicêtre, 94275, France

  • Azienda Ospedaliera Santobono Pausilipon - U.S.D. Centro Regionale Pediatrico Malattie della Coagulazione

    Naples, 80122, Italy

  • Azienda Ospedaliera di Rilievo Nazionale Santobono Pausilipon

    Naples, 80122, Italy

  • Beijing Children's Hospital, Capital Medical University

    Beijing, Beijing Municipality, 100045, China

  • Beijing Children's Hospital,Capital Medical University

    Beijing, Beijing Municipality, 100045, China

  • Belfast City Hospital

    Belfast, BT9 78B, United Kingdom

  • CMCV

    Ranipet, Tamil Nadu, 632517, India

  • Central Michigan University

    Detroit, Michigan, 48201, United States

  • Centre Hospitalier Universitaire de Lille-Institut Coeur Poumon

    Lille, 59037, France

  • Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu

    Nantes, 44000, France

  • Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu

    Nantes, Nantes, France

  • Centre of Oncology and Hematology, Vilnius University

    Vilnius, LT-08406, Lithuania

  • Centro Hospitalar Universitario De Santo Antonio E.P.E

    Porto, 4050-342, Portugal

  • Centro Multidisciplinario Para El Desarrollo Especializado De La Investigación Clínica En Yucatán S.C.P. (CEMDEICY S.C.P.)

    Mérida, 97130, Mexico

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Chengdu Women's and Children's Central Hospital

    Chengdu, Sichuan, 610074, China

  • Children University Clinical Hospital

    Riga, 1004, Latvia

  • Children's Healthcare Atlanta

    Atlanta, Georgia, 30329, United States

  • Children's Hospital Los Angeles - Endocrinology

    Los Angeles, California, 90027, United States

  • Children's Hospital, Zhejiang University School of Medicine-Hematology

    Huzhou, Zhejiang, 313200, China

  • Christian Medical College and Hospital

    Ludhiana, Punjab, 141008, India

  • Chung Shan Medical University Hospital

    Taichung, 402, Taiwan

  • Clinical Centre of Serbia, Institute for Haematology

    Belgrade, 11000, Serbia

  • Clinical Centre of Vojvodina

    Novi Sad, 21000, Serbia

  • Cliniques universitaires Saint-Luc - Service Hématologie

    Brussels, 1200, Belgium

  • Daejeon Eulji Medical Center, Eulji University

    Daejeon, 35233, South Korea

  • Dayton Children Hemostati Ctr

    Dayton, Ohio, 45404, United States

  • Ege Universitesi Tip Fakultesi

    Bornova-IZMIR, 35100, Turkey (Türkiye)

  • Ege Üniversitesi Hastanesi- Hematoloji

    Bornova-IZMIR, 35100, Turkey (Türkiye)

  • Evelina London Children's Hospital - Haemophilia

    London, SE1 7EH, United Kingdom

  • Fondazione IRCSS Ca' Granda Ospedale Maggiore Policlinico

    Milan, 20122, Italy

  • Gangdong Kyung Hee University Hospital

    Seoul, 05278, South Korea

  • Gazi University

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Gazi Üniversitesi Hastanesi- Hematoloji

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • HZRM Haemophilie-Zentrum Rhein Main GmbH

    Frankfurt am Main, 60596, Germany

  • Hacettepe Universitesi

    Ankara, 06100, Turkey (Türkiye)

  • Hacettepe Üniversitesi Hastanesi- Hematoloji

    Ankara, 06100, Turkey (Türkiye)

  • Haemotology, Nanfang Hospital, Southern Medical University

    Guangzhou, Guangdong, 510515, China

  • Hospices Civils de Lyon- Hopital Louis Pradel

    Bron, 69500, France

  • Hospital Ampang

    Ampang, Selangor, Selangor, 68000, Malaysia

  • Hospital Carlos Haya

    Málaga, 29010, Spain

  • Hospital Queen Elizabeth 1

    Kota Kinabalu, Sabah, 88586, Malaysia

  • Hospital Regional Universitario de Málaga

    Málaga, 29010, Spain

  • Hospital Sant Joan de Déu

    Esplugues Llobregat, 08950, Spain

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Vall d'Hebron

    Barcelona, 08035, Spain

  • IRCCS Humanitas Research Hospital - Centro Trombosi e Malattie Emorragiche

    Milan, 20089, Italy

  • Indiana Hemophilia-Thromb Ctr

    Indianapolis, Indiana, 46260, United States

  • Institut Oncologic "Prof. Dr. Ion Chiricuta" Cluj Napoca

    Cluj-Napoca, 400015, Romania

  • Institute of Hematology and Blood Diseases Hospital, Tianjin-Hematology

    Tianjin, Tianjin Municipality, 300020, China

  • Instytut Hematologii i Transfuzjologii

    Warsaw, Masovian Voivodeship, 02-776, Poland

  • Intytut Hematologii i Transfuzjologii

    Warsaw, Masovian Voivodeship, 02-776, Poland

  • Istanbul University Oncology Institute

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

  • Jichi Medical University Hospital_Hematology

    Tochigi, 329-0498, Japan

  • Jichi Medical University Hospital_Pediatrics

    Tochigi, 329-0498, Japan

  • Jinan Central Hospital

    Jinan, Shandong, 250062, China

  • Jinan Central Hospital

    Jinan, 250062, China

  • Jinan Central Hospital Affiliated to Shandong University

    Jinan, Shandong, 250062, China

  • King Faisal Specialist Hospital & Research Centre, Riyadh

    Riyadh, 12713, Saudi Arabia

  • Kyung Hee University Hospital at Gangdong

    Seoul, 05278, South Korea

  • McMaster University

    Hamilton, Ontario, L8N 3Z5, Canada

  • Nagoya University Hospital_Blood Transfusion

    Aichi, 466-8560, Japan

  • Nanfang Hospital, Southern Medical University-Haematology

    Guangzhou, Guangdong, 510515, China

  • Nara Medical University Hospital_Pediatrics

    Nara, 634-8522, Japan

  • National Center for Child Health and Development_Hematology

    Tokyo, 157-8535, Japan

  • National Taiwan University Hospital

    Taipei, 100, Taiwan

  • National Taiwan University Hospital_main

    Taipei, 100, Taiwan

  • Nirmal Hospital Pvt. Ltd.

    Surat, Gujarat, 395002, India

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Ospedale Pediatrico Bambino Ges

    Roma, 00165, Italy

  • Ota Memorial Hospital_Pediatrics

    Gunma, 373-8585, Japan

  • Penn State MS Hershey Med Ctr

    Hershey, Pennsylvania, 17033-2360, United States

  • Post Graduate Institute of Child Health

    Noida, Uttar Pradesh, 201303, India

  • Pädiatrische Onkologie-Hämatologie

    Lucerne, 6000, Switzerland

  • Rigshospitalet - Department of Haematology, 2081

    København Ø, 2100, Denmark

  • Royal Free Haemophilia Comprehensive Care Center

    London, NW3 2QG, United Kingdom

  • Royal Free Hospital - Haemophilia

    London, NW3 2QG, United Kingdom

  • Royal Hallamshire Hospital

    Sheffield, S10 2JF, United Kingdom

  • Rush University Med. Cntr

    Chicago, Illinois, 60612, United States

  • Rush University Medical Center

    Chicago, Illinois, 60612, United States

  • SHAT of Haematological Diseases EAD, Clinic of Paediatric Clinical Haematology

    Sofia, 1797, Bulgaria

  • SMS Medical College & Hospital

    Jaipur, Rajasthan, 302004, India

  • Sahyadri Clinical Research And Development Center

    Pune, Maharashtra, 411004, India

  • Saitama Children's Med Centre_Hematology-Oncology

    Saitama, 330-8777, Japan

  • Seth GS medical college and KEM Hospital

    Mumbai, Maharashtra, 400012, India

  • Seth GS medical college and KEM Hospital

    Mumbai, 400012, India

  • Severance Hospital, Yonsei University Health System

    Seoul, 03722, South Korea

  • Sheba MC - The Israeli National Hemophilia Center

    Tel Litwinsky, 52621, Israel

  • St Christopher Hosp for Child

    Philadelphia, Pennsylvania, 19134, United States

  • St James's CRF

    Dublin, Leinster, D08 A978, Ireland

  • St Joseph's Hospital Foundation

    Tampa, Florida, 33607, United States

  • St Thomas' Hospital - Haemostasis and Thrombosis Centre

    London, SE1 7EH, United Kingdom

  • Stradini Clinic of Oncology

    Riga, 1002, Latvia

  • Szpital Uniwersytecki, Oddzial Kliniczny Hematologii

    Krakow, 30-688, Poland

  • Taichung Veterans General Hospital

    Taichung, 407, Taiwan

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • Tokyo Medical Univ. Hospital_Laboratory Medicine

    Tokyo, 160-0023, Japan

  • Tongji Hospital, Tongji Medical College of HUST

    Wuhan, Hubei, 430030, China

  • Tongji Hospital, Tongji Medical College of HUST-Hematology

    Wuhan, Hubei, 430030, China

  • Trakya University

    Edirne, 22030, Turkey (Türkiye)

  • Trakya Üniversitesi Tıp Fakültesi Hastanesi-Hematoloji

    Edirne, 22030, Turkey (Türkiye)

  • UC Denver Hemoph & Thrombo Ctr

    Aurora, Colorado, 80045, United States

  • ULS De São João, E.P.E. - Hospital de São João

    Porto, 4200-319, Portugal

  • UMC Utrecht, Van Creveldkliniek

    Utrecht, 3584 CX, Netherlands

  • UZ Leuven - Kindergeneeskunde

    Leuven, 3000, Belgium

  • Unidade Local De Saúde De Coimbra, E.P.E.

    Coimbra, 3000-459, Portugal

  • Unidade Local De Saúde De São José, E.P.E.- Hospital D. Estefânia

    Lisbon, 1169-045, Portugal

  • Univ Hosp Cleveland Med Ctr

    Cleveland, Ohio, 44106, United States

  • Univ of Miami/SCCC

    Miami, Florida, 33136, United States

  • University Hospital of Wales - Haemophilia

    Cardiff, CF14 4XW, United Kingdom

  • University of Iowa_Iowa City

    Iowa City, Iowa, 52242, United States

  • Universitätsklinik für Hämatologie

    Bern, 3010, Switzerland

  • Universitätsklinik für Innere Medizin V

    Innsbruck, 6020, Austria

  • Universitätsklinik für Innere Medizin V

    Innsbruck, A 6020, Austria

  • Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie

    Bonn, 53127, Germany

  • Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie

    Zurich, 8091, Switzerland

  • Univerzitna Nemocnica Martin

    Martin, 036 59, Slovakia

  • Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa

    Lublin, 20-093, Poland

  • Uniwersytecki Szpital Kliniczny W Poznaniu

    Poznan, Greater Poland Voivodeship, 60-569, Poland

  • Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego

    Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

  • Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego

    Wroclaw, 50-556, Poland

  • Vanderbilt U Med Ctr_Nashville

    Nashville, Tennessee, 37212, United States

  • Vilnius University hospital Santaros klinikos

    Vilnius, 08661, Lithuania

  • Vivantes Netzwerk für Gesundheit GmbH - Vivantes Klinikum im Friedrichshain

    Berlin, 10249, Germany

  • Vranovska nemocnica, a.s.

    Vranov nad Topľou, 09327, Slovakia

  • Vseobecna nemocnica Rimavska Sobota

    Rimavská Sobota, 979 01, Slovakia

  • Wits Bara Clinical Trial Site

    Johannesburg, Gauteng, 2013, South Africa

  • Xiangya Hospital Central-South University

    Changsha, Hunan, 410008, China

  • Zentrum für Labormedizin

    Sankt Gallen, 9008, Switzerland

  • İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

Conditions

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