New injection could drastically cut bleeds for hemophilia patients

NCT ID NCT05053139

Summary

This study tested a new medicine called Mim8, given as a weekly or monthly injection, to prevent bleeding episodes in people with hemophilia A. It compared Mim8 to other standard treatments in 281 adults and adolescents, including those whose bodies make inhibitors against standard treatments. The goal was to see if Mim8 could better control the disease by replacing the missing clotting factor.

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Contacts and locations

Locations

  • AKH - Klin. Abt. f. Haematologie u. Haemostaseologie

    Vienna, 1090, Austria

  • Academisch Medisch Centrum

    Amsterdam, 1105 AZ, Netherlands

  • Acıbadem Adana Hastanesi-Hematoloji

    Adana, 01130, Turkey (Türkiye)

  • Akdeniz Universitesi

    Antalya, 01010, Turkey (Türkiye)

  • Akdeniz Üniversitesi Hastanesi- Hematoloji

    Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)

  • Ap-Hp-Hopital Necker-1

    Paris, 75015, France

  • Ap-Hp-Hopital de Bicetre-1

    Le Kremlin-Bicêtre, 94275, France

  • Arizona H&T Phoenix Child Hosp

    Phoenix, Arizona, 85016-7710, United States

  • Arnold Palmer Hospital for Children

    Orlando, Florida, 32806, United States

  • Arthur Bloom Haemophilia Centre

    Cardiff, CF14 4XW, United Kingdom

  • Augusta University

    Augusta, Georgia, 30912, United States

  • Balad Hlth Sys-Welmont CardCVA

    Kingsport, Tennessee, 37660, United States

  • Beijing Children's Hospital, Capital Medical University

    Beijing, Beijing Municipality, 100045, China

  • CHI Crumlin Haematology

    Dublin, D12 N512, Ireland

  • CMCV

    Ranipet, Tamil Nadu, 632517, India

  • Centre Hospitalier Universitaire de Bordeaux-Hopital Pellegrin

    Bordeaux, 33076, France

  • Centre Hospitalier Universitaire de Lille-Institut Coeur Poumon

    Lille, 59037, France

  • Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu

    Nantes, Nantes, France

  • Centre Hospitalier Universitaire de Rennes - Hopital Pontchaillou

    Rennes, 35033, France

  • Centro Hospitalar de São João_Porto

    Porto, 4200-319, Portugal

  • Centro Multidisciplinario Para El Desarrollo Especializado De La Investigación Clínica En Yucatán S.C.P. (CEMDEICY S.C.P.)

    Mérida, 97130, Mexico

  • Charlotte Maxeke Johannesburg Academic Hospital

    Parktown, Johannesburg, Gauteng, 2193, South Africa

  • Chengdu Women's and Children's Central Hospital

    Chengdu, Sichuan, 610074, China

  • Children HC Atlanta-Adv Pediat

    Atlanta, Georgia, 30329, United States

  • Children Oncohaematology department Children's Hospital,

    Vilnius, 08406, Lithuania

  • Children Regional Clinical Hospital

    Krasnodar, 350007, Russia

  • Children University Clinical Hospital

    Riga, 1004, Latvia

  • Children's Hosp-New Orleans

    New Orleans, Louisiana, 70118-5720, United States

  • Children's Hospital Los Angeles - Endocrinology

    Los Angeles, California, 90027, United States

  • Children's Hospital of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Children's Hospital, Zhejiang University School of Medicine

    Hangzhou, Zhejiang, 310052, China

  • Children's Medical Center_Dallas

    Dallas, Texas, 75235, United States

  • Christian medical college

    Ludhiana, Punjab, 141008, India

  • Chung Shan Medical University Hospital

    Taichung, 402, Taiwan

  • Cincinnati Child's Hsp Med Ctr

    Cincinnati, Ohio, 45229, United States

  • City Clinical Hospital #4 (Dnipro) - Haematology centre

    Dnipro, 49102, Ukraine

  • City out-patient clinic 37, City Hemophilia Centre

    Saint Petersburg, 191186, Russia

  • Clinical Centre of Serbia, Institute for Haematology

    Belgrade, 11000, Serbia

  • Clinical Centre of Vojvodina

    Novi Sad, 21000, Serbia

  • Cliniques universitaires Saint-Luc - Service Hématologie

    Brussels, 1200, Belgium

  • Cure 4 the Kids Foundation

    Las Vegas, Nevada, 89135, United States

  • Daejeon Eulji Medical Center, Eulji University

    Daejeon, 35233, South Korea

  • Dayton Children Hemostati Ctr

    Dayton, Ohio, 45404, United States

  • Dipartimento di Ematologia Univ. Firenze

    Florence, 50134, Italy

  • Eastern Health Authority

    St. John's, Newfoundland and Labrador, A1B 3V6, Canada

  • Ege Universitesi Tip Fakultesi

    Bornova-IZMIR, 35100, Turkey (Türkiye)

  • Ege Üniversitesi Hastanesi- Hematoloji

    Bornova-IZMIR, 35100, Turkey (Türkiye)

  • Erasmus MC

    Rotterdam, 3015 GD, Netherlands

  • Gazi University

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • Gazi Üniversitesi Hastanesi- Hematoloji

    Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)

  • HZRM Haemophilie-Zentrum Rhein Main GmbH

    Frankfurt am Main, 60596, Germany

  • Haemotology, Nanfang Hospital, Southern Medical University

    Guangzhou, Guangdong, 510515, China

  • Hemophilia Treatment Center

    Los Angeles, California, 90007, United States

  • Hopital Maisonneuve Rosemont

    Montreal, Quebec, HIT 2M4, Canada

  • Hospices Civils de Lyon- Hopital Louis Pradel-1

    Bron, 69500, France

  • Hospital Ampang

    Ampang, Selangor, 68000, Malaysia

  • Hospital Ampang

    Selangor Darul Ehsan, 68000, Malaysia

  • Hospital Queen Elizabeth 1

    Kota Kinabalu, Sabah, 88586, Malaysia

  • Hospital Regional Universitario de Málaga

    Málaga, 29009, Spain

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hospital Vall d'Hebron

    Barcelona, 08035, Spain

  • Hospital of LUHS "Kauno Klinikos"

    Kaunas, LT-50161, Lithuania

  • Hospital of the University of Occupational And Environmental Health Japan, Pediatrics

    Kitakyusyu-shi, Fukuoka, 807 8555, Japan

  • Hôpital Cardiologique Louis Pradel

    Bron, 69500, France

  • IRCCS Humanitas Research Hospital - Centro Trombosi e Malattie Emorragiche

    Milan, 20089, Italy

  • Indiana Hemophilia-Thromb Ctr

    Indianapolis, Indiana, 46260, United States

  • Institut Oncologic "Prof. Dr. Ion Chiricuta" Cluj Napoca

    Cluj-Napoca, 400015, Romania

  • Institute of Hematology and Blood Diseases Hospital, Tianjin-Hematology

    Tianjin, Tianjin Municipality, 300020, China

  • Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery

    Lviv, 79044, Ukraine

  • Institutul Clinic Fundeni

    Bucharest, 022328, Romania

  • Istanbul University Oncology Institute

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

  • Jichi Medical University Hospital_Hematology

    Tochigi, 329-0498, Japan

  • Jichi Medical University Hospital_Pediatrics

    Tochigi, 329-0498, Japan

  • Jinan Central Hospital

    Ji'Nan, Shandong, 250000, China

  • Jinan Central Hospital

    Jinan, Shandong, 250000, China

  • Kaohsiung Medical University Chung-Ho Memorial Hospital_Dept of Pediatrics

    Kaohsiung City, 807, Taiwan

  • King Faisal Specialist Hospital & Research Centre, Riyadh

    Riyadh, 12713, Saudi Arabia

  • Kyung Hee University Hospital at Gangdong

    Seoul, 05278, South Korea

  • London Health Sciences Center Ontario

    London, Ontario, N6A 5W9, Canada

  • McMaster University

    Hamilton, Ontario, L8N 3Z5, Canada

  • McMaster University Medical Center

    Hamilton, Ontario, L8N 3Z5, Canada

  • Memorial Health Univ Med Ctr

    Savannah, Georgia, 31404, United States

  • Michigan State University

    East Lansing, Michigan, 48823, United States

  • Morozovskaya municipal children hospital

    Moscow, 119049, Russia

  • Nagoya University Hospital_Blood Transfusion

    Aichi, 466-8560, Japan

  • Nanbu Medical Center & Children's Medical Center

    Okinawa, 901-1193, Japan

  • Nanfang Hospital, Southern Medical University-Haematology

    Guangzhou, Guangdong, 510515, China

  • National Center for Child Health and Development_Hematology

    Tokyo, 157-8535, Japan

  • National Medical Research institution of haemotology

    Moscow, 125167, Russia

  • National Taiwan University Hospital_Dept of Hematology

    Taipei, 100, Taiwan

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz

    Bratislava, 851 07, Slovakia

  • Nirmal Hospital Pvt. Ltd.

    Surat, Gujarat, 395002, India

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Oxford Haemophilia Comprehensive Care Center

    Oxford, OX3 7LJ, United Kingdom

  • Penn State MS Hershey Med Ctr

    Hershey, Pennsylvania, 17033-2360, United States

  • Post Graduate Institute of Child Health

    Noida, Uttar Pradesh, 201303, India

  • Providence Sacred Heart Medical Center & Children's Hospital

    Spokane, Washington, 99204, United States

  • Reg. State Budget Healthc. Inst. Regional Clinical Hospital

    Barnaul, 656024, Russia

  • Republican Hospital n.a. V. A. Baranov

    Petrozavodsk, 185019, Russia

  • Rigshospitalet - Department of Haematology, 2081

    København Ø, 2100, Denmark

  • Royal Free Haemophilia Comprehensive Care Centre

    London, NW3 2QG, United Kingdom

  • Royal University Hospital

    Saskatoon, Saskatchewan, S7N 0W8, Canada

  • Rush University Med. Cntr

    Chicago, Illinois, 60612, United States

  • SAHI Kuzbass Hospital(former Regional clinical hospital)

    Kemerovo, 650066, Russia

  • Saitama Children's Med Centre_Hematology-Oncology

    Saitama, 330-8777, Japan

  • Seth GS Medical College & KEM Hospital

    Mumbai, Maharashtra, 400012, India

  • Severance Hospital, Yonsei University Health System

    Seoul, 03722, South Korea

  • Sheba MC - The Israeli National Hemophilia Center

    Tel Litwinsky, 52621, Israel

  • Shizuoka Children's Hospital, Hematology-Oncology

    Shizuoka, 420-8660, Japan

  • Spitalul Clinic Municipal Filantropia Craiova

    Craiova, Dolj, 200143, Romania

  • Spitalul Clinic Municipal de Urgenta Timisoara

    Timișoara, 300254, Romania

  • St Christopher Hosp for Child

    Philadelphia, Pennsylvania, 19134, United States

  • St James's CRF

    Dublin, Leinster, D08 A978, Ireland

  • St Joseph's Hospital Foundation

    Tampa, Florida, 33607, United States

  • St Thomas' Hospital - Haemostasis and Thrombosis Centre

    London, SE1 7EH, United Kingdom

  • St. John Regional Hospital

    Saint John, New Brunswick, E2L 4L4, Canada

  • St. Jude Clinic Novant Health

    Charlotte, North Carolina, 28204, United States

  • Stradini Clinic of Oncology

    Riga, 1002, Latvia

  • Szpital Uniwersytecki, Oddzial Kliniczny Hematologii

    Krakow, Lesser Poland Voivodeship, 30-688, Poland

  • Taichung Veterans General Hospital

    Taichung, 407, Taiwan

  • The Children's Hospital, Zhejiang University school of medicine

    Hangzhou, Zhejiang, 310052, China

  • The First Affiliated Hospital of Soochow University

    Suzhou, Jiangsu, 215006, China

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • The Second Affiliated Hospital of Kunming Medical University

    Kunming, Yunnan, 650101, China

  • Tokyo Medical Univ. Hospital_Laboratory Medicine

    Tokyo, 160-0023, Japan

  • Tongji Hospital, Tongji Medical College of HUST

    Wuhan, Hubei, 430030, China

  • Tongji Hospital, Tongji Medical College of HUST-Hematology

    Wuhan, Hubei, 430030, China

  • Torrence Hemby Ped Hem/Onc Ctr

    Charlotte, North Carolina, 28203, United States

  • ULS São João, E.P.E.

    Porto, 4200-319, Portugal

  • UMC Utrecht, Van Creveldkliniek

    Utrecht, 3584 CX, Netherlands

  • UZ Antwerpen - UZA - Kinderhemato-Oncologie

    Edegem, 2650, Belgium

  • UZ Leuven - Kindergeneeskunde

    Leuven, 3000, Belgium

  • Unidade Local de Saúde de Coimbra, E.P.E.

    Coimbra, 3000-561, Portugal

  • Unidade Local de Saúde de Santo António, E.P.E

    Porto, 4099-001, Portugal

  • Unilabs Slovensko, s. r. o.

    Košice, 04001, Slovakia

  • Univ Hosp Cleveland Med Ctr

    Cleveland, Ohio, 44106, United States

  • Univ TX Hlth Sci Ctr Houston

    Houston, Texas, 77030, United States

  • Univ of Colorado Sch of Med

    Aurora, Colorado, 80045, United States

  • Univ of Miami/SCCC

    Miami, Florida, 33136, United States

  • Univ of NE Med Center_Omaha

    Omaha, Nebraska, 68105, United States

  • University Of Iowa

    Iowa City, Iowa, 52242, United States

  • University Of Michigan

    Ann Arbor, Michigan, 48109, United States

  • University of Iowa_Iowa City

    Iowa City, Iowa, 52242, United States

  • University of Manitoba

    Winnipeg, Manitoba, R3T 2N2, Canada

  • Universitätsklinik für Hämatologie

    Bern, 3010, Switzerland

  • Universitätsklinik für Innere Medizin V

    Innsbruck, 6020, Austria

  • Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie

    Bonn, 53127, Germany

  • Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie

    Zurich, 8091, Switzerland

  • Univerzitna Nemocnica Martin

    Martin, 036 59, Slovakia

  • Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa

    Lublin, 20-093, Poland

  • Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego

    Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

  • Ustav Hematologie a krevni tranfuze

    Prague, 128 20, Czechia

  • Vanderbilt Hemostasis Thrombosis Clinic

    Nashville, Tennessee, 37232-9830, United States

  • Vilnius University hospital Santaros klinikos

    Vilnius, LT-08661, Lithuania

  • Vivantes Netzwerk für Gesundheit GmbH - Vivantes Klinikum im Friedrichshain

    Berlin, 10249, Germany

  • Vranovska nemocnica, a.s.

    Vranov nad Topľou, 09327, Slovakia

  • Vseobecna nemocnica Rimavska Sobota

    Rimavská Sobota, 979 12, Slovakia

  • Washington University School of Medicine_St. Louis

    St Louis, Missouri, 63110, United States

  • Wits Bara Clinical Trial Site

    Johannesburg, Gauteng, 2013, South Africa

  • Xiangya Hospital Central-South University

    Changsha, Hunan, 410008, China

  • Zentrum für Labormedizin

    Sankt Gallen, 9008, Switzerland

  • İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü

    Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.