New injection could drastically cut bleeds for hemophilia patients
NCT ID NCT05053139
Summary
This study tested a new medicine called Mim8, given as a weekly or monthly injection, to prevent bleeding episodes in people with hemophilia A. It compared Mim8 to other standard treatments in 281 adults and adolescents, including those whose bodies make inhibitors against standard treatments. The goal was to see if Mim8 could better control the disease by replacing the missing clotting factor.
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Contacts and locations
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Locations
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AKH - Klin. Abt. f. Haematologie u. Haemostaseologie
Vienna, 1090, Austria
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Academisch Medisch Centrum
Amsterdam, 1105 AZ, Netherlands
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Acıbadem Adana Hastanesi-Hematoloji
Adana, 01130, Turkey (Türkiye)
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Akdeniz Universitesi
Antalya, 01010, Turkey (Türkiye)
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Akdeniz Üniversitesi Hastanesi- Hematoloji
Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)
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Ap-Hp-Hopital Necker-1
Paris, 75015, France
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Ap-Hp-Hopital de Bicetre-1
Le Kremlin-Bicêtre, 94275, France
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Arizona H&T Phoenix Child Hosp
Phoenix, Arizona, 85016-7710, United States
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Arnold Palmer Hospital for Children
Orlando, Florida, 32806, United States
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Arthur Bloom Haemophilia Centre
Cardiff, CF14 4XW, United Kingdom
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Augusta University
Augusta, Georgia, 30912, United States
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Balad Hlth Sys-Welmont CardCVA
Kingsport, Tennessee, 37660, United States
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Beijing Children's Hospital, Capital Medical University
Beijing, Beijing Municipality, 100045, China
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CHI Crumlin Haematology
Dublin, D12 N512, Ireland
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CMCV
Ranipet, Tamil Nadu, 632517, India
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Centre Hospitalier Universitaire de Bordeaux-Hopital Pellegrin
Bordeaux, 33076, France
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Centre Hospitalier Universitaire de Lille-Institut Coeur Poumon
Lille, 59037, France
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Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu
Nantes, Nantes, France
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Centre Hospitalier Universitaire de Rennes - Hopital Pontchaillou
Rennes, 35033, France
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Centro Hospitalar de São João_Porto
Porto, 4200-319, Portugal
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Centro Multidisciplinario Para El Desarrollo Especializado De La Investigación Clínica En Yucatán S.C.P. (CEMDEICY S.C.P.)
Mérida, 97130, Mexico
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Charlotte Maxeke Johannesburg Academic Hospital
Parktown, Johannesburg, Gauteng, 2193, South Africa
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Chengdu Women's and Children's Central Hospital
Chengdu, Sichuan, 610074, China
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Children HC Atlanta-Adv Pediat
Atlanta, Georgia, 30329, United States
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Children Oncohaematology department Children's Hospital,
Vilnius, 08406, Lithuania
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Children Regional Clinical Hospital
Krasnodar, 350007, Russia
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Children University Clinical Hospital
Riga, 1004, Latvia
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Children's Hosp-New Orleans
New Orleans, Louisiana, 70118-5720, United States
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Children's Hospital Los Angeles - Endocrinology
Los Angeles, California, 90027, United States
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Children's Hospital of Wisconsin
Milwaukee, Wisconsin, 53226, United States
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Children's Hospital, Zhejiang University School of Medicine
Hangzhou, Zhejiang, 310052, China
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Children's Medical Center_Dallas
Dallas, Texas, 75235, United States
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Christian medical college
Ludhiana, Punjab, 141008, India
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Chung Shan Medical University Hospital
Taichung, 402, Taiwan
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Cincinnati Child's Hsp Med Ctr
Cincinnati, Ohio, 45229, United States
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City Clinical Hospital #4 (Dnipro) - Haematology centre
Dnipro, 49102, Ukraine
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City out-patient clinic 37, City Hemophilia Centre
Saint Petersburg, 191186, Russia
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Clinical Centre of Serbia, Institute for Haematology
Belgrade, 11000, Serbia
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Clinical Centre of Vojvodina
Novi Sad, 21000, Serbia
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Cliniques universitaires Saint-Luc - Service Hématologie
Brussels, 1200, Belgium
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Cure 4 the Kids Foundation
Las Vegas, Nevada, 89135, United States
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Daejeon Eulji Medical Center, Eulji University
Daejeon, 35233, South Korea
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Dayton Children Hemostati Ctr
Dayton, Ohio, 45404, United States
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Dipartimento di Ematologia Univ. Firenze
Florence, 50134, Italy
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Eastern Health Authority
St. John's, Newfoundland and Labrador, A1B 3V6, Canada
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Ege Universitesi Tip Fakultesi
Bornova-IZMIR, 35100, Turkey (Türkiye)
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Ege Üniversitesi Hastanesi- Hematoloji
Bornova-IZMIR, 35100, Turkey (Türkiye)
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Erasmus MC
Rotterdam, 3015 GD, Netherlands
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Gazi University
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Gazi Üniversitesi Hastanesi- Hematoloji
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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HZRM Haemophilie-Zentrum Rhein Main GmbH
Frankfurt am Main, 60596, Germany
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Haemotology, Nanfang Hospital, Southern Medical University
Guangzhou, Guangdong, 510515, China
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Hemophilia Treatment Center
Los Angeles, California, 90007, United States
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Hopital Maisonneuve Rosemont
Montreal, Quebec, HIT 2M4, Canada
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Hospices Civils de Lyon- Hopital Louis Pradel-1
Bron, 69500, France
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Ampang
Selangor Darul Ehsan, 68000, Malaysia
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Hospital Queen Elizabeth 1
Kota Kinabalu, Sabah, 88586, Malaysia
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Hospital Regional Universitario de Málaga
Málaga, 29009, Spain
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Vall d'Hebron
Barcelona, 08035, Spain
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Hospital of LUHS "Kauno Klinikos"
Kaunas, LT-50161, Lithuania
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Hospital of the University of Occupational And Environmental Health Japan, Pediatrics
Kitakyusyu-shi, Fukuoka, 807 8555, Japan
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Hôpital Cardiologique Louis Pradel
Bron, 69500, France
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IRCCS Humanitas Research Hospital - Centro Trombosi e Malattie Emorragiche
Milan, 20089, Italy
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Indiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, 46260, United States
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Institut Oncologic "Prof. Dr. Ion Chiricuta" Cluj Napoca
Cluj-Napoca, 400015, Romania
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Institute of Hematology and Blood Diseases Hospital, Tianjin-Hematology
Tianjin, Tianjin Municipality, 300020, China
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Institute of blood pathology and transfusion medicine of NAMSU - General and haematol. surgery
Lviv, 79044, Ukraine
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Institutul Clinic Fundeni
Bucharest, 022328, Romania
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Istanbul University Oncology Institute
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
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Jichi Medical University Hospital_Hematology
Tochigi, 329-0498, Japan
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Jichi Medical University Hospital_Pediatrics
Tochigi, 329-0498, Japan
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Jinan Central Hospital
Ji'Nan, Shandong, 250000, China
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Jinan Central Hospital
Jinan, Shandong, 250000, China
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Kaohsiung Medical University Chung-Ho Memorial Hospital_Dept of Pediatrics
Kaohsiung City, 807, Taiwan
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King Faisal Specialist Hospital & Research Centre, Riyadh
Riyadh, 12713, Saudi Arabia
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Kyung Hee University Hospital at Gangdong
Seoul, 05278, South Korea
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London Health Sciences Center Ontario
London, Ontario, N6A 5W9, Canada
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McMaster University
Hamilton, Ontario, L8N 3Z5, Canada
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McMaster University Medical Center
Hamilton, Ontario, L8N 3Z5, Canada
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Memorial Health Univ Med Ctr
Savannah, Georgia, 31404, United States
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Michigan State University
East Lansing, Michigan, 48823, United States
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Morozovskaya municipal children hospital
Moscow, 119049, Russia
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Nagoya University Hospital_Blood Transfusion
Aichi, 466-8560, Japan
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Nanbu Medical Center & Children's Medical Center
Okinawa, 901-1193, Japan
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Nanfang Hospital, Southern Medical University-Haematology
Guangzhou, Guangdong, 510515, China
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National Center for Child Health and Development_Hematology
Tokyo, 157-8535, Japan
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National Medical Research institution of haemotology
Moscow, 125167, Russia
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National Taiwan University Hospital_Dept of Hematology
Taipei, 100, Taiwan
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Nemocnica sv. Cyrila a Metoda, UNB,Klinika hemat. a transfuz
Bratislava, 851 07, Slovakia
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Nirmal Hospital Pvt. Ltd.
Surat, Gujarat, 395002, India
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Ogikubo Hospital_Pediatries & Blood
Tokyo, 167-0035, Japan
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Oxford Haemophilia Comprehensive Care Center
Oxford, OX3 7LJ, United Kingdom
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Penn State MS Hershey Med Ctr
Hershey, Pennsylvania, 17033-2360, United States
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Post Graduate Institute of Child Health
Noida, Uttar Pradesh, 201303, India
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Providence Sacred Heart Medical Center & Children's Hospital
Spokane, Washington, 99204, United States
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Reg. State Budget Healthc. Inst. Regional Clinical Hospital
Barnaul, 656024, Russia
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Republican Hospital n.a. V. A. Baranov
Petrozavodsk, 185019, Russia
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Rigshospitalet - Department of Haematology, 2081
København Ø, 2100, Denmark
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Royal Free Haemophilia Comprehensive Care Centre
London, NW3 2QG, United Kingdom
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Royal University Hospital
Saskatoon, Saskatchewan, S7N 0W8, Canada
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Rush University Med. Cntr
Chicago, Illinois, 60612, United States
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SAHI Kuzbass Hospital(former Regional clinical hospital)
Kemerovo, 650066, Russia
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Saitama Children's Med Centre_Hematology-Oncology
Saitama, 330-8777, Japan
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Seth GS Medical College & KEM Hospital
Mumbai, Maharashtra, 400012, India
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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Sheba MC - The Israeli National Hemophilia Center
Tel Litwinsky, 52621, Israel
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Shizuoka Children's Hospital, Hematology-Oncology
Shizuoka, 420-8660, Japan
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Spitalul Clinic Municipal Filantropia Craiova
Craiova, Dolj, 200143, Romania
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Spitalul Clinic Municipal de Urgenta Timisoara
Timișoara, 300254, Romania
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St Christopher Hosp for Child
Philadelphia, Pennsylvania, 19134, United States
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St James's CRF
Dublin, Leinster, D08 A978, Ireland
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St Joseph's Hospital Foundation
Tampa, Florida, 33607, United States
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St Thomas' Hospital - Haemostasis and Thrombosis Centre
London, SE1 7EH, United Kingdom
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St. John Regional Hospital
Saint John, New Brunswick, E2L 4L4, Canada
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St. Jude Clinic Novant Health
Charlotte, North Carolina, 28204, United States
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Stradini Clinic of Oncology
Riga, 1002, Latvia
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Szpital Uniwersytecki, Oddzial Kliniczny Hematologii
Krakow, Lesser Poland Voivodeship, 30-688, Poland
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Taichung Veterans General Hospital
Taichung, 407, Taiwan
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The Children's Hospital, Zhejiang University school of medicine
Hangzhou, Zhejiang, 310052, China
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The First Affiliated Hospital of Soochow University
Suzhou, Jiangsu, 215006, China
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The Hospital for Sick Children
Toronto, Ontario, M5G 1X8, Canada
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The Second Affiliated Hospital of Kunming Medical University
Kunming, Yunnan, 650101, China
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Tokyo Medical Univ. Hospital_Laboratory Medicine
Tokyo, 160-0023, Japan
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Tongji Hospital, Tongji Medical College of HUST
Wuhan, Hubei, 430030, China
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Tongji Hospital, Tongji Medical College of HUST-Hematology
Wuhan, Hubei, 430030, China
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Torrence Hemby Ped Hem/Onc Ctr
Charlotte, North Carolina, 28203, United States
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ULS São João, E.P.E.
Porto, 4200-319, Portugal
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UMC Utrecht, Van Creveldkliniek
Utrecht, 3584 CX, Netherlands
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UZ Antwerpen - UZA - Kinderhemato-Oncologie
Edegem, 2650, Belgium
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UZ Leuven - Kindergeneeskunde
Leuven, 3000, Belgium
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Unidade Local de Saúde de Coimbra, E.P.E.
Coimbra, 3000-561, Portugal
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Unidade Local de Saúde de Santo António, E.P.E
Porto, 4099-001, Portugal
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Unilabs Slovensko, s. r. o.
Košice, 04001, Slovakia
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Univ Hosp Cleveland Med Ctr
Cleveland, Ohio, 44106, United States
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Univ TX Hlth Sci Ctr Houston
Houston, Texas, 77030, United States
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Univ of Colorado Sch of Med
Aurora, Colorado, 80045, United States
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Univ of Miami/SCCC
Miami, Florida, 33136, United States
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Univ of NE Med Center_Omaha
Omaha, Nebraska, 68105, United States
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University Of Iowa
Iowa City, Iowa, 52242, United States
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University Of Michigan
Ann Arbor, Michigan, 48109, United States
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University of Iowa_Iowa City
Iowa City, Iowa, 52242, United States
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University of Manitoba
Winnipeg, Manitoba, R3T 2N2, Canada
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Universitätsklinik für Hämatologie
Bern, 3010, Switzerland
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Universitätsklinik für Innere Medizin V
Innsbruck, 6020, Austria
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Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie
Bonn, 53127, Germany
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Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie
Zurich, 8091, Switzerland
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Univerzitna Nemocnica Martin
Martin, 036 59, Slovakia
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Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa
Lublin, 20-093, Poland
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Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego
Wroclaw, Lower Silesian Voivodeship, 50-556, Poland
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Ustav Hematologie a krevni tranfuze
Prague, 128 20, Czechia
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Vanderbilt Hemostasis Thrombosis Clinic
Nashville, Tennessee, 37232-9830, United States
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Vilnius University hospital Santaros klinikos
Vilnius, LT-08661, Lithuania
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Vivantes Netzwerk für Gesundheit GmbH - Vivantes Klinikum im Friedrichshain
Berlin, 10249, Germany
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Vranovska nemocnica, a.s.
Vranov nad Topľou, 09327, Slovakia
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Vseobecna nemocnica Rimavska Sobota
Rimavská Sobota, 979 12, Slovakia
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Washington University School of Medicine_St. Louis
St Louis, Missouri, 63110, United States
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Wits Bara Clinical Trial Site
Johannesburg, Gauteng, 2013, South Africa
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Xiangya Hospital Central-South University
Changsha, Hunan, 410008, China
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Zentrum für Labormedizin
Sankt Gallen, 9008, Switzerland
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İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
Conditions
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