New Long-Term treatment aims to stop bleeds in haemophilia patients
NCT ID NCT05685238
Summary
This study is testing the long-term safety and effectiveness of a new medicine called Mim8 for people with haemophilia A. Mim8 is designed to prevent bleeding episodes by helping the blood to clot. The study will follow participants for up to 5.5 years to see how well the treatment works and monitor for any side effects.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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A.O.U. Città della Salute e della Scienza di Torino-Ospedale
Torino, 10126, Italy
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A.O.U. Policlinico Umberto I
Rome, Lazio, 00161, Italy
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A.O.U. Policlinico Umberto I
Rome, 00161, Italy
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AKH - Klin. Abt. f. Haematologie u. Haemostaseologie
Vienna, 1090, Austria
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AOU Careggi Firenze
Florence, 50134, Italy
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Acıbadem Adana Hastanesi-Hematoloji
Adana, 01130, Turkey (Türkiye)
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Akdeniz Universitesi
Antalya, 01010, Turkey (Türkiye)
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Akdeniz Üniversitesi Hastanesi- Hematoloji
Antalya, Konyaaltı/ Antalya, 01010, Turkey (Türkiye)
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AmsterdamUMC AMC
Amsterdam, 1105 AZ, Netherlands
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Ap-Hp-Hopital de Bicetre
Le Kremlin-Bicêtre, 94275, France
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Ap-Hp-Hopital de Bicetre-1
Le Kremlin-Bicêtre, 94275, France
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Azienda Ospedaliera Santobono Pausilipon - U.S.D. Centro Regionale Pediatrico Malattie della Coagulazione
Naples, 80122, Italy
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Azienda Ospedaliera di Rilievo Nazionale Santobono Pausilipon
Naples, 80122, Italy
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Beijing Children's Hospital, Capital Medical University
Beijing, Beijing Municipality, 100045, China
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Beijing Children's Hospital,Capital Medical University
Beijing, Beijing Municipality, 100045, China
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Belfast City Hospital
Belfast, BT9 78B, United Kingdom
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CMCV
Ranipet, Tamil Nadu, 632517, India
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Central Michigan University
Detroit, Michigan, 48201, United States
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Centre Hospitalier Universitaire de Lille-Institut Coeur Poumon
Lille, 59037, France
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Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu
Nantes, 44000, France
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Centre Hospitalier Universitaire de Nantes-Hopital Hotel-Dieu
Nantes, Nantes, France
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Centre of Oncology and Hematology, Vilnius University
Vilnius, LT-08406, Lithuania
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Centro Hospitalar Universitario De Santo Antonio E.P.E
Porto, 4050-342, Portugal
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Centro Multidisciplinario Para El Desarrollo Especializado De La Investigación Clínica En Yucatán S.C.P. (CEMDEICY S.C.P.)
Mérida, 97130, Mexico
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Charlotte Maxeke Johannesburg Academic Hospital
Parktown, Johannesburg, Gauteng, 2193, South Africa
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Chengdu Women's and Children's Central Hospital
Chengdu, Sichuan, 610074, China
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Children University Clinical Hospital
Riga, 1004, Latvia
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Children's Healthcare Atlanta
Atlanta, Georgia, 30329, United States
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Children's Hospital Los Angeles - Endocrinology
Los Angeles, California, 90027, United States
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Children's Hospital, Zhejiang University School of Medicine-Hematology
Huzhou, Zhejiang, 313200, China
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Christian Medical College and Hospital
Ludhiana, Punjab, 141008, India
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Chung Shan Medical University Hospital
Taichung, 402, Taiwan
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Clinical Centre of Serbia, Institute for Haematology
Belgrade, 11000, Serbia
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Clinical Centre of Vojvodina
Novi Sad, 21000, Serbia
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Cliniques universitaires Saint-Luc - Service Hématologie
Brussels, 1200, Belgium
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Daejeon Eulji Medical Center, Eulji University
Daejeon, 35233, South Korea
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Dayton Children Hemostati Ctr
Dayton, Ohio, 45404, United States
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Ege Universitesi Tip Fakultesi
Bornova-IZMIR, 35100, Turkey (Türkiye)
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Ege Üniversitesi Hastanesi- Hematoloji
Bornova-IZMIR, 35100, Turkey (Türkiye)
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Evelina London Children's Hospital - Haemophilia
London, SE1 7EH, United Kingdom
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Fondazione IRCSS Ca' Granda Ospedale Maggiore Policlinico
Milan, 20122, Italy
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Gangdong Kyung Hee University Hospital
Seoul, 05278, South Korea
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Gazi University
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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Gazi Üniversitesi Hastanesi- Hematoloji
Ankara, Beşevler/Ankara, 06500, Turkey (Türkiye)
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HZRM Haemophilie-Zentrum Rhein Main GmbH
Frankfurt am Main, 60596, Germany
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Hacettepe Universitesi
Ankara, 06100, Turkey (Türkiye)
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Hacettepe Üniversitesi Hastanesi- Hematoloji
Ankara, 06100, Turkey (Türkiye)
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Haemotology, Nanfang Hospital, Southern Medical University
Guangzhou, Guangdong, 510515, China
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Hospices Civils de Lyon- Hopital Louis Pradel
Bron, 69500, France
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Hospital Ampang
Ampang, Selangor, Selangor, 68000, Malaysia
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Hospital Carlos Haya
Málaga, 29010, Spain
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Hospital Queen Elizabeth 1
Kota Kinabalu, Sabah, 88586, Malaysia
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Hospital Regional Universitario de Málaga
Málaga, 29010, Spain
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Hospital Sant Joan de Déu
Esplugues Llobregat, 08950, Spain
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Hospital Universitario La Paz
Madrid, 28046, Spain
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Hospital Vall d'Hebron
Barcelona, 08035, Spain
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IRCCS Humanitas Research Hospital - Centro Trombosi e Malattie Emorragiche
Milan, 20089, Italy
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Indiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, 46260, United States
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Institut Oncologic "Prof. Dr. Ion Chiricuta" Cluj Napoca
Cluj-Napoca, 400015, Romania
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Institute of Hematology and Blood Diseases Hospital, Tianjin-Hematology
Tianjin, Tianjin Municipality, 300020, China
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Instytut Hematologii i Transfuzjologii
Warsaw, Masovian Voivodeship, 02-776, Poland
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Intytut Hematologii i Transfuzjologii
Warsaw, Masovian Voivodeship, 02-776, Poland
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Istanbul University Oncology Institute
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
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Jichi Medical University Hospital_Hematology
Tochigi, 329-0498, Japan
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Jichi Medical University Hospital_Pediatrics
Tochigi, 329-0498, Japan
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Jinan Central Hospital
Jinan, Shandong, 250062, China
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Jinan Central Hospital
Jinan, 250062, China
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Jinan Central Hospital Affiliated to Shandong University
Jinan, Shandong, 250062, China
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King Faisal Specialist Hospital & Research Centre, Riyadh
Riyadh, 12713, Saudi Arabia
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Kyung Hee University Hospital at Gangdong
Seoul, 05278, South Korea
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McMaster University
Hamilton, Ontario, L8N 3Z5, Canada
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Nagoya University Hospital_Blood Transfusion
Aichi, 466-8560, Japan
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Nanfang Hospital, Southern Medical University-Haematology
Guangzhou, Guangdong, 510515, China
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Nara Medical University Hospital_Pediatrics
Nara, 634-8522, Japan
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National Center for Child Health and Development_Hematology
Tokyo, 157-8535, Japan
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National Taiwan University Hospital
Taipei, 100, Taiwan
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National Taiwan University Hospital_main
Taipei, 100, Taiwan
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Nirmal Hospital Pvt. Ltd.
Surat, Gujarat, 395002, India
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Ogikubo Hospital_Pediatries & Blood
Tokyo, 167-0035, Japan
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Ospedale Pediatrico Bambino Ges
Roma, 00165, Italy
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Ota Memorial Hospital_Pediatrics
Gunma, 373-8585, Japan
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Penn State MS Hershey Med Ctr
Hershey, Pennsylvania, 17033-2360, United States
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Post Graduate Institute of Child Health
Noida, Uttar Pradesh, 201303, India
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Pädiatrische Onkologie-Hämatologie
Lucerne, 6000, Switzerland
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Rigshospitalet - Department of Haematology, 2081
København Ø, 2100, Denmark
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Royal Free Haemophilia Comprehensive Care Center
London, NW3 2QG, United Kingdom
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Royal Free Hospital - Haemophilia
London, NW3 2QG, United Kingdom
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Royal Hallamshire Hospital
Sheffield, S10 2JF, United Kingdom
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Rush University Med. Cntr
Chicago, Illinois, 60612, United States
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Rush University Medical Center
Chicago, Illinois, 60612, United States
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SHAT of Haematological Diseases EAD, Clinic of Paediatric Clinical Haematology
Sofia, 1797, Bulgaria
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SMS Medical College & Hospital
Jaipur, Rajasthan, 302004, India
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Sahyadri Clinical Research And Development Center
Pune, Maharashtra, 411004, India
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Saitama Children's Med Centre_Hematology-Oncology
Saitama, 330-8777, Japan
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Seth GS medical college and KEM Hospital
Mumbai, Maharashtra, 400012, India
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Seth GS medical college and KEM Hospital
Mumbai, 400012, India
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Severance Hospital, Yonsei University Health System
Seoul, 03722, South Korea
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Sheba MC - The Israeli National Hemophilia Center
Tel Litwinsky, 52621, Israel
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St Christopher Hosp for Child
Philadelphia, Pennsylvania, 19134, United States
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St James's CRF
Dublin, Leinster, D08 A978, Ireland
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St Joseph's Hospital Foundation
Tampa, Florida, 33607, United States
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St Thomas' Hospital - Haemostasis and Thrombosis Centre
London, SE1 7EH, United Kingdom
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Stradini Clinic of Oncology
Riga, 1002, Latvia
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Szpital Uniwersytecki, Oddzial Kliniczny Hematologii
Krakow, 30-688, Poland
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Taichung Veterans General Hospital
Taichung, 407, Taiwan
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The Hospital for Sick Children
Toronto, Ontario, M5G 1X8, Canada
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Tokyo Medical Univ. Hospital_Laboratory Medicine
Tokyo, 160-0023, Japan
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Tongji Hospital, Tongji Medical College of HUST
Wuhan, Hubei, 430030, China
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Tongji Hospital, Tongji Medical College of HUST-Hematology
Wuhan, Hubei, 430030, China
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Trakya University
Edirne, 22030, Turkey (Türkiye)
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Trakya Üniversitesi Tıp Fakültesi Hastanesi-Hematoloji
Edirne, 22030, Turkey (Türkiye)
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UC Denver Hemoph & Thrombo Ctr
Aurora, Colorado, 80045, United States
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ULS De São João, E.P.E. - Hospital de São João
Porto, 4200-319, Portugal
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UMC Utrecht, Van Creveldkliniek
Utrecht, 3584 CX, Netherlands
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UZ Leuven - Kindergeneeskunde
Leuven, 3000, Belgium
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Unidade Local De Saúde De Coimbra, E.P.E.
Coimbra, 3000-459, Portugal
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Unidade Local De Saúde De São José, E.P.E.- Hospital D. Estefânia
Lisbon, 1169-045, Portugal
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Univ Hosp Cleveland Med Ctr
Cleveland, Ohio, 44106, United States
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Univ of Miami/SCCC
Miami, Florida, 33136, United States
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University Hospital of Wales - Haemophilia
Cardiff, CF14 4XW, United Kingdom
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University of Iowa_Iowa City
Iowa City, Iowa, 52242, United States
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Universitätsklinik für Hämatologie
Bern, 3010, Switzerland
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Universitätsklinik für Innere Medizin V
Innsbruck, 6020, Austria
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Universitätsklinik für Innere Medizin V
Innsbruck, A 6020, Austria
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Universitätsklinikum Bonn - Institut für Experimentelle Hämatologie
Bonn, 53127, Germany
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Universitätsspital Zürich - Klinik für Medizinische Onkologie und Hämatologie
Zurich, 8091, Switzerland
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Univerzitna Nemocnica Martin
Martin, 036 59, Slovakia
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Uniwersytecki Szpital Dzieciecy, Dzial Krwiolecznictwa
Lublin, 20-093, Poland
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Uniwersytecki Szpital Kliniczny W Poznaniu
Poznan, Greater Poland Voivodeship, 60-569, Poland
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Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego
Wroclaw, Lower Silesian Voivodeship, 50-556, Poland
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Uniwersytecki Szpital Kliniczny im. J.Mikulicza-Radeckiego
Wroclaw, 50-556, Poland
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Vanderbilt U Med Ctr_Nashville
Nashville, Tennessee, 37212, United States
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Vilnius University hospital Santaros klinikos
Vilnius, 08661, Lithuania
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Vivantes Netzwerk für Gesundheit GmbH - Vivantes Klinikum im Friedrichshain
Berlin, 10249, Germany
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Vranovska nemocnica, a.s.
Vranov nad Topľou, 09327, Slovakia
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Vseobecna nemocnica Rimavska Sobota
Rimavská Sobota, 979 01, Slovakia
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Wits Bara Clinical Trial Site
Johannesburg, Gauteng, 2013, South Africa
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Xiangya Hospital Central-South University
Changsha, Hunan, 410008, China
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Zentrum für Labormedizin
Sankt Gallen, 9008, Switzerland
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İstanbul Üniversitesi İstanbul Tıp Fakültesi Hastanesi- Onkoloji Enstitüsü
Capa-ISTANBUL, Capa-ISTANBUL, 34093, Turkey (Türkiye)
Conditions
Explore the condition pages connected to this study.