Can immune therapy help rare muscle disorder?

NCT ID NCT06599697

First seen Jun 27, 2026 · Last updated Aug 06, 2026 · Updated 2 times

Summary

This phase 2 trial tests whether intravenous immunoglobulin (IVIG) can help people with a rare autoimmune muscle disease called anti-HMGCR immune-mediated necrotizing myopathy. Twelve participants will receive either IVIG or a placebo every 4 weeks for 12 weeks, then all may receive IVIG in an open-label extension. The main goal is to see if IVIG lowers muscle enzyme levels and is safe.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
Intravenous immunoglobulin (IVIG)
What this could lead to
If it works, this could point toward a treatment for a rare muscle disease that causes weakness and damage.
What could go wrong
This is a very small early-phase trial with only 12 people, so results may not apply widely. IVIG can cause side effects like headache, fever, or allergic reactions.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Johns Hopkins University

    NOT_YET_RECRUITING

    Baltimore, Maryland, 21218, United States

  • University of Alabama at Birmingham

    RECRUITING

    Birmingham, Alabama, 35233, United States

  • University of Pittsburgh

    RECRUITING

    Pittsburgh, Pennsylvania, 15260, United States

  • University of Texas Health Science Center at Houston

    RECRUITING

    Houston, Texas, 77030, United States

  • University of Washington

    ACTIVE_NOT_RECRUITING

    Seattle, Washington, 98195, United States