Diabetes drug could fight rare brain cancer in kids

NCT ID NCT07226453

First seen Jun 24, 2026 · Last updated Aug 14, 2026 · Updated 5 times

Summary

This study tests whether metformin, a common diabetes medicine, can help children and young adults with a rare brain tumor called PFA ependymoma that has come back. About 30 participants will take metformin and have surgery and imaging to see if the drug changes certain proteins in the tumor and slows its growth. The goal is to find a new way to control this hard-to-treat cancer.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
Metformin (Glucophage)
What this could lead to
If successful, this could point toward a new treatment option for a rare brain tumor that currently has few options after standard therapy.
What could go wrong
This is a small, early-phase trial with only 30 participants. Metformin is not a standard cancer drug, and it may not slow tumor growth or improve outcomes.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Children's National Hospital

    NOT_YET_RECRUITING

    Washington D.C., District of Columbia, 20010, United States

  • Duke University Medical Center

    RECRUITING

    Durham, North Carolina, 27710, United States

  • Johns Hopkins Hospital

    RECRUITING

    Baltimore, Maryland, 21287, United States

  • Joseph M. Sanzari Children's Hospital at Hackensack University Medical Center

    NOT_YET_RECRUITING

    Hackensack, New Jersey, 07601, United States

  • St. Jude Children's Research Hospital

    NOT_YET_RECRUITING

    Memphis, Tennessee, 38105, United States

  • St. Louis Children's Hospital, Washington University in St. Louis

    RECRUITING

    St Louis, Missouri, 63110, United States

  • UCSF Benioff Children's Hospital, University of California, San Francisco

    RECRUITING

    San Francisco, California, 94143, United States

  • University of Alabama at Birmingham, Children's of Alabama

    NOT_YET_RECRUITING

    Birmingham, Alabama, 35233, United States

  • University of Michigan, C.S. Mott Children's Hospital

    NOT_YET_RECRUITING

    Ann Arbor, Michigan, 48109, United States

  • University of Utah, Primary Children's Hospital

    NOT_YET_RECRUITING

    Salt Lake City, Utah, 84113, United States