Could a liver drug help kids and adults with rare metabolic disorder?

This study tests whether sodium phenylbutyrate (ACER-001), a drug already approved for another condition, can help people with MCAD deficiency caused by a specific gene mutation. About 24 participants aged 4 and older will take the drug and be monitored for safety and how well it keeps their blood sugar stable. The goal is to see if this drug can reduce the risk of dangerous low blood sugar episodes.