Experimental liposomal chemo shows promise in kids with relapsed leukemia

NCT ID NCT02879643

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This pilot study tested a liposomal form of the chemotherapy drug vincristine (Marqibo) combined with standard UK ALL R3 chemotherapy in 29 children, adolescents, and young adults with relapsed acute lymphoblastic leukemia. The main goal was to see if it was safe and tolerable at different doses. The study also looked at how often serious side effects or treatment delays occurred.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

vincristine sulfate liposome injection (Marqibo)

What this could lead to

If successful, this could offer a new chemotherapy option for children and young adults with relapsed acute lymphoblastic leukemia.

What could go wrong

This is a small, early-phase safety study with only 29 participants. It may not lead to better outcomes, and there are risks of serious side effects like nerve damage or infections.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute lymphoblastic leukemia childhood acute lymphoblastic leukemia lymphoblastic lymphoma mixed phenotype acute leukemia Precursor Cell Lymphoblastic Leukemia-Lymphoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • All Children's Hospital

    St. Petersburg, Florida, 33701, United States

  • British Columbia Children's Hospital

    Vancouver, British Columbia, V6H 3V4, Canada

  • CS Mott Children's Hospital, Ann Arbor

    Ann Arbor, Michigan, 48109, United States

  • Children's Healthcare of Atlanta at Egleston

    Atlanta, Georgia, 30322, United States

  • Children's Hospital New York-Presbyterian

    New York, New York, 10032, United States

  • Children's Hospital Orange County

    Orange, California, 92868, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's Hospitals and Clinics of Minnesota

    Minneapolis, Minnesota, 55404, United States

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010, United States

  • Childrens Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Cincinnati Children's Hospital

    Cincinnati, Ohio, 45229, United States

  • Cook Children's Medical Center

    Fort Worth, Texas, 76104, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • Lady Cilento Children's Hospital

    South Brisbane, Queensland, 4101, Australia

  • Levine Children's Hospital

    Charlotte, North Carolina, 28203, United States

  • Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Medical College of Wisconsin

    Milwaukee, Wisconsin, 53226, United States

  • Monroe Carell Jr. Children's Hospital at Vanderbilt

    Nashville, Tennessee, 37232, United States

  • National Cancer Institute, Pediatric Oncology Branch

    Bethesda, Maryland, 20892, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Oregon Health & Science University

    Portland, Oregon, 97239, United States

  • Primary Children's Hospital

    Salt Lake City, Utah, 84113, United States

  • Rainbow Babies & Children's Hospital

    Cleveland, Ohio, 44106, United States

  • Royal Children's Hospital, Melbourne

    Parkville, Victoria, 3052, Australia

  • Sainte-Justine University Hospital Center

    Montréal, Québec, H3T-1C5, Canada

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

  • Sidney Kimmel Cancer Center at Johns Hopkins

    Baltimore, Maryland, 21231, United States

  • Sydney Children's Hospital

    Randwick, New South Wales, 2031, Australia

  • Texas Children's Cancer Center, Baylor

    Houston, Texas, 77030, United States

  • The Children's Hospital at Westmead

    Westmead, New South Wales, 2145, Australia

  • The Children's Hospital, University of Colorado

    Aurora, Colorado, 80045, United States

  • UCSF School of Medicine

    San Francisco, California, 94158, United States

  • University of Miami

    Miami, Florida, 33136, United States

  • University of Texas Southwestern Medical Center

    Dallas, Texas, 75235, United States