New pill targets genetic weakness in Hard-to-Treat blood cancers

NCT ID NCT04603001

First seen Jul 02, 2026 · Last updated Jul 02, 2026

Summary

This study tests an experimental oral drug called LY3410738 in people with advanced blood cancers such as acute myeloid leukemia (AML) and myelodysplastic syndrome (MDS) that have specific IDH1 or IDH2 gene mutations. The drug is designed to block the mutated IDH proteins that help cancer grow. The trial aims to find the safest dose and measure how well the drug works, both alone and in combination with other treatments.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

LY3410738

What this could lead to

If successful, this could provide a new targeted treatment option for people with certain blood cancers that have IDH1 or IDH2 mutations.

What could go wrong

This is an early phase 1 trial, so the drug may not work as hoped or could have unexpected side effects. The results are preliminary and may not lead to a widely available treatment.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute myeloid leukemia chronic myelomonocytic leukemia myelodysplastic syndrome Myelodysplastic Syndromes Myeloproliferative Disorders myeloproliferative neoplasm

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

More trials for these conditions

Other studies related to the condition(s) this trial covers.

Contacts and locations

Locations

  • Asan Medical Center

    Seoul, Seoul-teukbyeolsi [Seoul], 05505, South Korea

  • BC Cancer Vancouver

    Vancouver, British Columbia, V5Z 4E6, Canada

  • Centre Hospitalier Lyon Sud

    Pierre-Bénite, 69495, France

  • Centre hospitalier universitaire de Haut Leveque

    Pessac, 33604, France

  • China Medical University Hospital

    Taichung, 40447, Taiwan

  • City of Hope National Medical Center

    Duarte, California, 91010, United States

  • Clinico Y Provincial Barcelona

    Barcelona, 8036, Spain

  • Cliniques universitaires Saint-Luc

    Brussels, 1200, Belgium

  • H Lee Moffitt Cancer Center

    Tampa, Florida, 33612-9497, United States

  • Helsinki University Hospital - Comprehensive Cancer Center (HYKS - Syöpäkeskus)

    Helsinki, 00290, Finland

  • Hopital Saint Louis

    Paris, 75010, France

  • Hospital Universitario Fundación Jiménez Díaz

    Madrid, 28040, Spain

  • Hospital Universitario La Fe de Valencia

    Valencia, 46026, Spain

  • Institut Claudius Regaud

    Toulouse, 31059, France

  • Institut Paoli-Calmettes

    Marseille, 13273, France

  • Jewish General Hospital

    Montreal, Quebec, H3T 1E2, Canada

  • Linear Clinical Research

    Nedlands, Western Australia, 6009, Australia

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

  • Medizinische Hochschule Hanover

    Hanover, Lower Saxony, 30625, Germany

  • Memorial Sloan Kettering Cancer Center

    New York, New York, 10065, United States

  • National Taiwan University Hospital

    Taipei, 10002, Taiwan

  • National University Cancer Institute

    Singapore, 119228, Singapore

  • Northwestern University

    Chicago, Illinois, 60611, United States

  • Peter MacCallum Cancer Centre

    Melbourne, Victoria, 3000, Australia

  • Princess Margaret Hospital

    Toronto, Ontario, M5G2M9, Canada

  • Rambam Medical Center

    Haifa, 3109601, Israel

  • Roswell Park Cancer Institute

    Buffalo, New York, 14263-0002, United States

  • Samsung Medical Center

    Seoul, Seoul-teukbyeolsi [Seoul], 06351, South Korea

  • Seoul National University Hospital

    Seoul, 03080, South Korea

  • Singapore General Hospital

    Singapore, 169608, Singapore

  • The Alfred Hospital

    Melbourne, Victoria, 3004, Australia

  • UCLA Medical Center

    Los Angeles, California, 90095, United States

  • University of California, Davis - Health Systems

    Sacramento, California, 95817, United States

  • University of Chicago Hospital

    Chicago, Illinois, 60637, United States

  • University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, 27514, United States

  • University of Texas MD Anderson Cancer Center

    Houston, Texas, 77030, United States

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States