Hope for friedreich ataxia: Long-Term vatiquinone safety trial underway
NCT ID NCT05515536
First seen Nov 01, 2025 · Last updated May 13, 2026 · Updated 26 times
Summary
This study looks at the long-term safety of a drug called vatiquinone in people with Friedreich ataxia who have already taken it in earlier studies. About 130 participants will be followed for up to 3 years to monitor side effects and track changes in their movement and coordination. The goal is to see if vatiquinone remains safe and may help control the disease over time.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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CBR Neurogenetic Research Clinic, University of Auckland
Auckland, 1023, New Zealand
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CHU Sainte-Justine
Montreal, Quebec, H3T1C5, Canada
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Centre de Recherche du Centre Hospitalier de l'Université de Montreal (CRCHUM)
Montreal, Quebec, H2X 0A9, Canada
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Department of Neurology and Hertie-Institute for Clinical Brain Research German Center of Neurodegenerative Diseases (DZNE)
Tübingen, 72076, Germany
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Hospital Sant Joan de Déu Barcelona Unidad de Enfermedades Neuromusculares
Barcelona, 08950, Spain
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Hôpital Pitié-Salpêtrière, Institut du Cerveau (Paris Brain Institute)
Paris, 75646, France
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Murdoch Children's Research Institute
Parkville, Victoria, 3052, Australia
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Ospedale Pediatrico Bambino Gesu' IRCCS
Roma, 00165, Italy
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The Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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UCLA
Los Angeles, California, 90095, United States
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University of Campinas (UNICAMP) - School of Medical Sciences, Dept of Neurology
São Paulo, 13083-887, Brazil
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University of Florida
Gainesville, Florida, 32608, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of South Florida
Tampa, Florida, 33612, United States
Conditions
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