New hope for duchenne: Long-Term drug safety trial underway

NCT ID NCT07209332

First seen Nov 01, 2025

Summary

This study looks at the long-term safety of an experimental drug called WVE-N531 in people with Duchenne muscular dystrophy (DMD) who have already taken it in a previous study. About 175 participants will receive the drug and be monitored for side effects, heart and lung function, and muscle strength. The goal is to see if the drug remains safe and effective over time.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Istiklal Hospital/ Clinical Research Unit

    Amman, Jordan

  • Oxford Children's Hospital, Oxford University Hospitals NHS Foundation Trust

    Headington, Oxford, OX3 9DU, United Kingdom

  • The Specialty Hospital (TSH)/ Advanced Clinical Center

    Amman, Jordan

Conditions

The condition(s) this trial relates to.

Duchenne muscular dystrophy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.