New study tracks Long-Term safety of DMD drug AGAMREE in boys
NCT ID NCT06564974
First seen Feb 28, 2026 · Last updated May 14, 2026 · Updated 9 times
Summary
This study monitors the long-term safety of the drug vamorolone (AGAMREE) in boys aged 2 and older with Duchenne muscular dystrophy. Researchers will track growth, bone health, heart function, and quality of life over time. The goal is to better understand the drug's risks and benefits when used for extended periods.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Arkansas Childrens Hospital
RECRUITINGLittle Rock, Arkansas, 72202, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Atrium Health Neurosciences Institute
RECRUITINGCharlotte, North Carolina, 28207, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital Los Angeles
NOT_YET_RECRUITINGLos Angeles, California, 90027, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital of Philadelphia (CHOP)
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Wisconsin
NOT_YET_RECRUITINGMilwaukee, Wisconsin, 53226, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Cincinnati Children's Hospital Medical Center
RECRUITINGCincinnati, Ohio, 45229, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Duke University Medical Center and Childrens Health Center
RECRUITINGDurham, North Carolina, 27710, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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FDI Clinical Research
RECRUITINGSan Juan, Puerto Rico, 00927, Puerto Rico
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Helen DeVos Children's Hospital
RECRUITINGGrand Rapids, Michigan, 49503, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Indiana University Health - Riley Hospital for Children
NOT_YET_RECRUITINGIndianapolis, Indiana, 46202, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Johns Hopkins All Children's Hospital
NOT_YET_RECRUITINGSt. Petersburg, Florida, 33701, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Lurie Children's Hospital of Chicago
RECRUITINGChicago, Illinois, 60611, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Nemours Children's Hospital
RECRUITINGOrlando, Florida, 32827, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Neurology Rare Disease Center - Neurology & Neuromuscular Care Center
RECRUITINGDenton, Texas, 76208, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Nicklaus Children's Hospital
RECRUITINGMiami, Florida, 33155, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Penn State Milton S. Hershey Medical Center- Penn State Hershey Neuroscience Institute
RECRUITINGHershey, Pennsylvania, 17033, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Phoenix Children's Hospital
RECRUITINGPhoenix, Arizona, 85016, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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San Jorge Children's Hospital
RECRUITINGSan Juan, Puerto Rico, 00912, Puerto Rico
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Seattle Children's Hospital
RECRUITINGSeattle, Washington, 98105, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Stanford University
NOT_YET_RECRUITINGPalo Alto, California, 94305, United States
Contact Phone: •••-•••-••••
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The University of Texas Health Science Center at San Antonio
RECRUITINGSan Antonio, Texas, 78229, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of California, Davis
NOT_YET_RECRUITINGSacramento, California, 95817, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Florida Clinical and Translational Science Institue
NOT_YET_RECRUITINGGainesville, Florida, 32610, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Kansas Medical Center
RECRUITINGKansas City, Kansas, 66205, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Massachusetts Memorial Medical Center
RECRUITINGNorth Worcester, Massachusetts, 01655, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Texas Southwestern Medical Center
RECRUITINGDallas, Texas, 75235, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Virginia Health System (UVAHS) - Pediatric Neuromuscular Center
RECRUITINGCharlottesville, Virginia, 22903, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.