New drug trial aims to halt liver damage in genetic disease

NCT ID NCT06165341

Summary

This study is testing a drug called fazirsiran for people with liver disease caused by Alpha-1 antitrypsin deficiency. The drug aims to reduce the buildup of an abnormal protein that causes liver scarring. About 50 adults with early-stage liver scarring will receive either the drug or a placebo for two years to see if it safely slows or stops disease progression.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Bon Secours St. Mary's Hospital

    RECRUITING

    Newport, Virginia, 23602-4414, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Boston Medical Center

    RECRUITING

    Boston, Massachusetts, 02118-2335, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • CCA Hospital Braga

    RECRUITING

    Braga, 4710-243, Portugal

    Contact

  • Centro Hospitalar de Universitário de Santo António E.P.E

    RECRUITING

    Porto, 4099-001, Portugal

    Contact

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  • Charité - Campus Virchow-Klinikum

    RECRUITING

    Berlin, 13353, Germany

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Columbia University Irving Medical Center

    RECRUITING

    New York, New York, 10032-3722, United States

    Contact

  • Fondazione IRCCS Policlinico San Matteo

    RECRUITING

    Pavia, 27100, Italy

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  • Hannover Medical School

    RECRUITING

    Hanover, 30625, Germany

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  • Henry Ford Health System

    RECRUITING

    Novi, Michigan, 48377-3600, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hopital PONTCHAILLOU CHU de Rennes

    RECRUITING

    Rennes, 35000, France

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hospital Dr. Nélio Mendonça

    RECRUITING

    Funchal, 9000-168, Portugal

    Contact Phone: •••-•••-••••

    Contact

  • Hospital Universitario Virgen del Rocio - PPDS

    RECRUITING

    Seville, 41018, Spain

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hôpital Paul Brousse

    RECRUITING

    Val-de-Marne, 94800, France

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hôpital de La Croix Rousse

    RECRUITING

    Lyon, 69317, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • ID Clinic Arkadiusz Pisula

    WITHDRAWN

    Mysłowice, 41-400, Poland

  • Indiana University School of Medicine-Indianapolis

    RECRUITING

    Indianapolis, Indiana, 46202-2266, United States

    Contact

    Contact Phone: •••-•••-••••

  • Inspiration Research Limited

    RECRUITING

    Toronto, Ontario, M5T 3A9, Canada

    Contact

    Contact Phone: •••-•••-••••

  • KABEG - Klinikum Klagenfurt Am Wörthersee

    RECRUITING

    Klagenfurt, 9020, Austria

    Contact

  • Karolinska Universitetssjukhuset Huddinge

    RECRUITING

    Huddinge, 14186, Sweden

    Contact Phone: •••-•••-••••

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  • King's College Hospital

    RECRUITING

    London, SE5 9RS, United Kingdom

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  • LKH-Universitätsklinikum Graz

    RECRUITING

    Graz, 8036, Austria

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic - PPDS

    RECRUITING

    Phoenix, Arizona, 85054-4502, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mayo Clinic PPDS

    RECRUITING

    Rochester, Minnesota, 55905, United States

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  • NYU Langone Medical Center

    RECRUITING

    New York, New York, 10016-6402, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Peak Gastroenterology Associates

    RECRUITING

    Colorado Springs, Colorado, 80907, United States

    Contact

    Contact Phone: •••-•••-••••

  • Penn State Health Milton S. Hershey Medical Center

    RECRUITING

    Hershey, Pennsylvania, 17033-2360, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Schiff Center for Liver Diseases/University of Miami

    RECRUITING

    Miami, Florida, 33136, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • St Joseph's Hospital and Medical Center

    RECRUITING

    Phoenix, Arizona, 85013-4224, United States

    Contact

    Contact Phone: •••-•••-••••

  • Texas Liver Institute American Research Corporation

    RECRUITING

    San Antonio, Texas, 78215, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • UCLA Pulmonary and Critical Care

    RECRUITING

    Los Angeles, California, 90095-3075, United States

    Contact

    Contact Phone: •••-•••-••••

  • UZ Antwerpen

    RECRUITING

    Antwerp, 2650, Belgium

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • UZ Leuven

    RECRUITING

    Leuven, 3000, Belgium

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University Hospitals Cleveland Medical Center

    RECRUITING

    Cleveland, Ohio, 44106-1716, United States

    Contact

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  • University Of Iowa Hospitals And Clinics

    RECRUITING

    Iowa City, Iowa, 52242-1009, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Arizona Thomas D. Boyer Liver Institute

    RECRUITING

    Tucson, Arizona, 85724-0001, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of California Benioff Children's Hospital

    RECRUITING

    San Francisco, California, 94143-2203, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of California San Diego

    RECRUITING

    La Jolla, California, 92037-1337, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Michigan Hospital - 1500 E Medical Center Dr

    RECRUITING

    Ann Arbor, Michigan, 48109, United States

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  • Universitätsklinikum Tübingen

    RECRUITING

    Tübingen, 72076, Germany

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  • Universitätsklinikum der RWTH Aachen

    RECRUITING

    Aachen, 52074, Germany

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Universitätsspital Bern

    RECRUITING

    Bern, 3010, Switzerland

    Contact

    Contact Phone: •••-•••-••••

Conditions

Explore the condition pages connected to this study.