Scientists track rare muscle disease to pave way for future treatments

NCT ID NCT03842878

Summary

This study aimed to better understand how Limb-Girdle Muscular Dystrophy 2I (LGMD2I) progresses over time. Researchers followed 52 patients for up to 2 years, measuring their walking ability, muscle strength, heart function, and overall mobility. The goal was to gather detailed information about the disease's course to help design better future treatment trials.

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Contacts and locations

Locations

  • Dr Tanya Stojkovic

    Paris, 75013, France

  • Pr John Vissing

    Copenhagen, DK-2100, Denmark

  • Pr Volker Straub

    Newcastle, NE1 3BZ, United Kingdom

Conditions

Explore the condition pages connected to this study.