First treatment tested for babies with deadly artery hardening disease
NCT ID NCT05734196
Summary
This study is testing a new enzyme replacement therapy called INZ-701 in infants with rare genetic disorders that cause dangerous calcium buildup in arteries and weak bones. The main goal is to check if the treatment is safe and well-tolerated in babies under one year old. Researchers will also measure how the drug works in the body and whether it improves key markers of the disease.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Boston Children's Hospital
WITHDRAWNBoston, Massachusetts, 02115, United States
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Hospital Sant Joan de Déu
TERMINATEDBarcelona, Spain
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Nationwide Children's Hospital
RECRUITINGColumbus, Ohio, 43205, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Rady Children's Hospital
RECRUITINGSan Diego, California, 92123, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Royal Manchester Children's Hospital
TERMINATEDManchester, M13 9WL, United Kingdom
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The Children's Hospital of Philadelphia
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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The University of Utah
WITHDRAWNSalt Lake City, Utah, 84108, United States
Conditions
Explore the condition pages connected to this study.