Brain injection trial offers hope for halting Huntington's

NCT ID NCT05541627

Summary

This early-stage study is testing a one-time gene therapy called AB-1001, delivered directly into the brain, in a small group of adults with early Huntington's disease. The main goals are to see if the treatment is safe and to look for early signs that it might slow the disease. Researchers will monitor participants for five years after the procedure to track their health and brain changes.

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Contacts and locations

Locations

  • Institut du Cerveau (ICM), Hôpital La Pitié Salpêtrière APHP

    Paris, Île-de-France Region, 75013, France

Conditions

Explore the condition pages connected to this study.