Hope for duchenne: new cell therapy shows promise in Long-Term trial
NCT ID NCT04428476
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests the long-term safety and effectiveness of a cell therapy called deramiocel (CAP-1002) in people with Duchenne muscular dystrophy who completed the earlier HOPE-2 trial. Participants receive an infusion of deramiocel every 3 months for about 5 years, with the option to continue until the drug is available commercially. The goal is to see if regular treatment can help maintain upper limb function and keep side effects manageable.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Children's Hospital Colorado
Aurora, Colorado, 80045, United States
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Children's Hospital Wisconsin
Milwaukee, Wisconsin, 53226, United States
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Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, 45229, United States
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University of California, Davis
Sacramento, California, 95817, United States
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Washington University
St Louis, Missouri, 63110, United States