New hope for kids with rare bleeding disorder

NCT ID NCT01467427

Summary

This trial tested a new, long-acting medication (N9-GP) to control bleeding in children with severe hemophilia B. It involved 25 boys under 13 who had previously used other treatments. The main goals were to see if the drug was safe, how well it prevented and treated bleeds, and how long it lasted in the body.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for HAEMOPHILIA B are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • Ap-Hp-Hopital Necker-1

    Paris, 75015, France

  • Ap-Hp-Hopital de Bicetre-1

    Le Kremlin-Bicêtre, 94275, France

  • Augusta University

    Augusta, Georgia, 30912, United States

  • Basingstoke & North Hampshire Hospital - Centre for Haemophilia, Haemostasis and Thrombosis

    Basingstoke, RG24 9NA, United Kingdom

  • Birmingham Children's Hospital

    Birmingham, B4 6NH, United Kingdom

  • Children's Hospital Los Angeles - Endocrinology

    Los Angeles, California, 90027, United States

  • Children's Hospital of Michigan

    Detroit, Michigan, 48201, United States

  • Children's Hospitals And Clinics Of Minnesota

    Minneapolis, Minnesota, 55404, United States

  • Children's Hosptl Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's Medical Center_Dallas

    Dallas, Texas, 75235, United States

  • Childrens National Medical Ctr

    Washington D.C., District of Columbia, 20010-2978, United States

  • Clinical Hospital Centre Split, Firule, Paediatric Haem. Dpt

    Split, 21 000, Croatia

  • Coagulation Research Center

    Duisburg, 47051, Germany

  • Colorado Hemophilia & Thrombosis Center

    Aurora, Colorado, 80045, United States

  • Dayton Children Hemostati Ctr

    Dayton, Ohio, 45404, United States

  • Emory University_Atlanta_1

    Atlanta, Georgia, 30322, United States

  • Hemorio-Fundarj

    Rio de Janeiro, 20211-030, Brazil

  • Hospital das Clínicas da Faculdade de Medicina da USP

    São Paulo, São Paulo, 05403-000, Brazil

  • Hôpital de la Timone

    Marseille, 13385, France

  • Istituto di Medicina Int. A. Bianchi Bonomi Univ. Milano

    Milan, MI, 20124, Italy

  • John Radcliffe Hospital

    Oxford, OX3 9DU, United Kingdom

  • Johns Hopkins University_Baltimore_3

    Baltimore, Maryland, 21205, United States

  • Leicester Royal Infirmary

    Leicester, LE1 5WW, United Kingdom

  • Leicester Royal Infirmary - Haemostasis & Thrombosis Unit

    Leicester, LE1 5WW, United Kingdom

  • Maimonides Medical Center

    Brooklyn, New York, 11220, United States

  • Medizinische Hochschule Hannover - Pädiatrische Hämato-, Onko- und Hämostasiologie

    Hanover, 30625, Germany

  • Mount Sinai Medical Center

    New York, New York, 10029, United States

  • National Blood Centre

    Kuala Lumpur, 50400, Malaysia

  • National Taiwan University Children's Hospital

    Taipei, 100, Taiwan

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Necmettin Erbakan University Pediatric Hematology

    Konya, 42090, Turkey (Türkiye)

  • Nucleo de Pesquisa Instituto Pele Pequeno Principe

    Curitiba, Paraná, 80250-060, Brazil

  • Ogikubo Hospital_Pediatries & Blood

    Tokyo, 167-0035, Japan

  • Rutgers-Robert Wood Johnson Medical School

    New Brunswick, New Jersey, 08901, United States

  • Shizuoka Children's Hospital, Hematology-Oncology

    Shizuoka, 420-8660, Japan

  • St Thomas' Hospital

    London, SE1 7EH, United Kingdom

  • St Thomas' Hospital - Haemostasis and Thrombosis Centre

    London, SE1 7EH, United Kingdom

  • St. Marianna University School of Medicine Hospital_Pediatrics

    Kanagawa, 216-8511, Japan

  • Texas Children's Hospital_Houston

    Houston, Texas, 77030, United States

  • The Children's Mercy Hospital

    Kansas City, Missouri, 64108-4619, United States

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • UC Davis Medical Center

    Sacramento, California, 95817, United States

  • Univ Hosp Cleveland Med Ctr

    Cleveland, Ohio, 44106, United States

  • Univ Oklahoma Sci Ctr OK City

    Oklahoma City, Oklahoma, 73104, United States

  • Univ TX Hlth Sci Ctr Houston

    Houston, Texas, 77030, United States

  • Univ of NE Med Center_Omaha

    Omaha, Nebraska, 68198, United States

  • Universidade Estadual de Campinas

    Campinas, São Paulo, 13081-970, Brazil

  • University Of Iowa

    Iowa City, Iowa, 52242, United States

  • University Of Louisville_Louisville_0

    Louisville, Kentucky, 40202, United States

  • University of Miami Hospital & Clinics

    Miami, Florida, 33136, United States

  • Vanderbilt Hemostasis Thrombosis Clinic

    Nashville, Tennessee, 37232, United States

Conditions

Explore the condition pages connected to this study.