New study tracks heart changes in rare MPS disorders

NCT ID NCT07361536

First seen Jan 26, 2026 · Last updated May 15, 2026 · Updated 15 times

Summary

This study looks at how heart and blood vessel problems develop in people with MPS types I and IVA. Researchers will use yearly ultrasounds, blood draws, and urine tests for 4 years to track changes and find markers that could guide future treatments. The study involves 240 participants, including people with MPS and healthy volunteers.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children'S Hospital of Orange County

    RECRUITING

    Orange, California, 92868, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Saint Louis University

    NOT_YET_RECRUITING

    St Louis, Missouri, 63104, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Minnesota

    NOT_YET_RECRUITING

    Minneapolis, Minnesota, 55455, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.