New drug trial aims to help kids with rare genetic disorders grow taller
NCT ID NCT06668805
Summary
This study is testing whether a drug called vosoritide can help children with Turner syndrome, SHOX deficiency, or Noonan syndrome grow taller. It's for kids aged 3-12 who haven't grown enough despite receiving standard growth hormone treatment. Researchers will compare three different doses to see which works best and is safest over six months, with some children followed for up to 15 years.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Contact
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Locations
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Angers University Hospital Center
RECRUITINGAngers, Maine-et-Loire, 49 933, France
Contact Email: •••••@•••••
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Atrium Health Carolinas Medical Center
RECRUITINGCharlotte, North Carolina, 28203, United States
Contact Email: •••••@•••••
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Azienda Ospedaliero Universitaria - Ospedale Pediatrico Meyer
RECRUITINGFlorence, Florence, Firenze, Italy
Contact Phone: •••-•••-•••• Email: •••••@•••••
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CHU de Toulouse - Hôpital des Enfants
RECRUITINGToulouse, Occitanie, France
Contact Email: •••••@•••••
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Central University Hospital of Asturias
NOT_YET_RECRUITINGOviedo, Principality of Asturias, 33011, Spain
Contact Email: •••••@•••••
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Children's Hospital Colorado
RECRUITINGAurora, Colorado, 80045, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital at Montefiore
RECRUITINGThe Bronx, New York, 10467, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Hospital of Orange County Main Campus - Orange
RECRUITINGOrange, California, 92868, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's Medical Center Dallas
RECRUITINGDallas, Texas, 75235, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Children's National Medical Center
RECRUITINGWashington D.C., District of Columbia, 20010, United States
Contact Email: •••••@•••••
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Hôpital Robert-Debré
RECRUITINGParis, Paris, 75019, France
Contact Email: •••••@•••••
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Hôpital de la Timone
RECRUITINGMarseille, Bouches-du-Rhône, 13385, France
Contact Email: •••••@•••••
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IRCCS Istituto Giannina Gaslini
NOT_YET_RECRUITINGGenova, Genoa, 16147, Italy
Contact Email: •••••@•••••
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Icahn School of Medicine at Mount Sinai
RECRUITINGNew York, New York, 10029, United States
Contact Email: •••••@•••••
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Kentucky Children's Hospital
RECRUITINGLexington, Kentucky, 40506, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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M Health Fairview Pediatric Specialty Clinic - Explorer
RECRUITINGMinneapolis, Minnesota, 55454, United States
Contact Email: •••••@•••••
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Murdoch Children's Research Institute
RECRUITINGParkville, Victoria, 3052, Australia
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Nemours Children's Hospital, Delaware (Alfred I. Dupont Hospital for Children)
RECRUITINGWilmington, Delaware, 19803, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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New York Medical College
RECRUITINGBoston, Massachusetts, 02115, United States
Contact Email: •••••@•••••
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Nicklaus Children's Hospital
NOT_YET_RECRUITINGMiami, Florida, 33155, United States
Contact Email: •••••@•••••
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South Paris University Hospitals - Bicetre Hospital
RECRUITINGLe Kremlin-Bicêtre, Paris, 94270, France
Contact Email: •••••@•••••
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St. Luke's Children's Endocrinology and Diabetes
RECRUITINGBoise, Idaho, 83712, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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University of Texas Health Science Center at Houston (UT Health)
RECRUITINGHouston, Texas, 77030, United States
Contact Email: •••••@•••••
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Vanderbilt University Medical Center
RECRUITINGNashville, Tennessee, 37232-2578, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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