Could genomic screening at birth unlock early treatment for rare diseases?

NCT ID NCT05990179

First seen Sep 30, 2025 · Last updated May 09, 2026 · Updated 32 times

Summary

This study explores whether genomic sequencing can help screen newborns for rare genetic conditions beyond the standard newborn screening. Researchers will invite families of 100,000 newborns to participate, offering optional screening for additional treatable or emerging conditions. The goal is to see if this approach is practical and can lead to earlier diagnosis and care.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Columbia University Irving Medical Center/NYP

    RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.