One-Shot gene therapy aims to halt blindness

NCT ID NCT05748873

Summary

This early-stage study is testing the safety of a single gene therapy injection, called SPVN06, for adults with an advanced form of retinitis pigmentosa caused by specific genetic mutations. The goal is to see if delivering a working gene directly to the retina can slow or stop the progression of vision loss. Researchers will monitor participants for up to five years to check for side effects and any early signs that the treatment helps preserve vision.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Bascom Palmer Eye Institute/University of Miami

    RECRUITING

    Miami, Florida, 33136, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • CHNO XV-XX Paris - CIC 1423

    RECRUITING

    Paris, 75012, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Casey Eye Institute

    RECRUITING

    Portland, Oregon, 97239, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mass Eye and Ear

    RECRUITING

    Boston, Massachusetts, 02114, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Retina Foundation of the Southwest

    RECRUITING

    Dallas, Texas, 75231, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • UPMC Eye Center

    RECRUITING

    Pittsburgh, Pennsylvania, 15213, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.