Gene injection trial aims to restore sight in rare blindness disease

NCT ID NCT07303296

Summary

This study is testing whether a gene therapy called GS010 can improve vision in people with Leber hereditary optic neuropathy, a rare genetic condition that causes sudden vision loss. Researchers will inject the therapy into both eyes of 14 participants to see if it helps restore visual acuity and retinal function. The study will compare two different doses and follow patients for 1.5 years to assess safety and effectiveness.

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Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

Locations

  • Hopital national des quinze-vingts

    RECRUITING

    Paris, 75012, France

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.