First human trial for gene therapy targeting rare heart disease

NCT ID NCT07426419

Summary

This early-stage trial is testing a new, single-dose gene therapy called AFTX-201 for adults with a specific inherited form of heart failure. The main goal is to see if the treatment is safe and well-tolerated. Researchers will also look for early signs that it might improve heart function and quality of life in participants.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

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Conditions

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