One-Shot gene therapy trial offers new hope for rare disease
NCT ID NCT06539624
Summary
This study is testing a new, one-time gene therapy called EXG110 for people with Fabry disease, a rare genetic disorder. Researchers want to find a safe dose and see if it can help control the disease by improving kidney and heart function. The study is enrolling a small group of adults and children aged 7 and older.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Children's Hospital, Zhejiang University School of Medicine
RECRUITINGHangzhou, Zhejiang, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Shanghai Children's Medical Center
RECRUITINGShanghai, Shanghai Municipality, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Conditions
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