First-in-Human gene therapy injection aims to halt blindness

NCT ID NCT06460844

Summary

This is an early safety study testing a single injection of an experimental gene therapy called RTx-015 into the eye. It aims to see if the treatment is safe for adults with retinitis pigmentosa or choroideremia, two inherited diseases that cause vision loss. Researchers will give the injection to up to 18 people in small groups, starting with a low dose, and follow their health closely for five years.

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Contacts and locations

Locations

  • Retina Consultants of Texas Research Centers

    Bellaire, Texas, 77401, United States

  • Retina Vitreous Associates Medical Group

    Beverly Hills, California, 90211, United States

  • UCI Alpha Clinic

    Orange, California, 92868, United States

  • UPMC Vision Institute

    Pittsburgh, Pennsylvania, 15221, United States

Conditions

Explore the condition pages connected to this study.