Gene therapy trial offers hope for kids with severe epilepsy

NCT ID NCT06112275

Summary

This early-stage study is testing a one-time gene therapy called ETX101 in young children with Dravet syndrome, a severe form of genetic epilepsy. The main goals are to see if the treatment is safe and if it can reduce the number and severity of seizures over one year. The study is small and is currently not enrolling new participants.

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Contacts and locations

Locations

  • The Royal Children's Hospital

    Melbourne, Australia

Conditions

Explore the condition pages connected to this study.