Gene therapy trial offers hope for kids with severe epilepsy
NCT ID NCT06112275
Summary
This early-stage study is testing a one-time gene therapy called ETX101 in young children with Dravet syndrome, a severe form of genetic epilepsy. The main goals are to see if the treatment is safe and if it can reduce the number and severity of seizures over one year. The study is small and is currently not enrolling new participants.
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Contacts and locations
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Locations
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The Royal Children's Hospital
Melbourne, Australia
Conditions
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