First-Ever gene therapy trial aims to restore vision in children with albinism

NCT ID NCT07313618

Summary

This early-stage study is testing a new gene therapy called JWK010 for children aged 5-12 with a specific type of albinism (OCA1). The goal is to see if a single injection into the eye is safe and can help the body produce pigment, which may improve vision and eye structure. Researchers will carefully monitor for side effects while measuring changes in vision, eye color, and eye movement.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • West China Hospital, Sichuan University

    RECRUITING

    Chengdu, Sichuan, 610041, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.