Gene therapy watch: 5-Year safety check for inherited blindness treatment
NCT ID NCT04312672
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study followed 42 people who received a gene therapy for X-linked retinitis pigmentosa, an inherited eye disease that causes blindness. The goal was to check the treatment's safety over up to 5 years. Researchers also looked at whether patients' vision and ability to move around in low light improved.
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Leeds Teaching Hospitals NHS Trust
Leeds, LS9 7TF, United Kingdom
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Massachusetts Eye and Ear Infirmary
Boston, Massachusetts, 02114, United States
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Moorfields Eye Hospital
London, EC1V 9EL, United Kingdom
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Univ of Michigan Medical Center
Ann Arbor, Michigan, 48105, United States
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University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, 15213, United States