Gene-Editing breakthrough: could a single injection fix sickle cell?
NCT ID NCT07000318
First seen May 15, 2026 · Last updated May 15, 2026
Summary
This early-stage study tests a new gene therapy called CS-206 for people with severe sickle cell disease. The treatment uses a patient's own blood stem cells, which are modified with a gene-editing tool to correct the disease. Five participants aged 12 to 18 will receive a single dose, and researchers will monitor safety and whether it reduces painful crises.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for SICKLE CELL DISEASE are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Children's Hospital of Fudan University
Shanghai, Shanghai Municipality, 201102, China
Conditions
Explore the condition pages connected to this study.