Gene therapy shows promise for rare Blindness-Causing eye disease

This early-stage study tested a gene therapy called CPK850 in 12 adults with a rare inherited eye disease (RLBP1 retinitis pigmentosa) that causes progressive vision loss and night blindness. The treatment was injected under the retina to deliver a working copy of the faulty gene, aiming to improve the eye's ability to adapt to darkness. The main goals were to check safety and see if vision function could be restored.