Gene therapy offers hope for rare blindness

This study tests a new gene therapy, CPK850, for people with a rare inherited eye disease called RLBP1 retinitis pigmentosa, which causes progressive vision loss and trouble seeing in the dark. The treatment is given as a single injection under the retina to deliver a working copy of the faulty gene. The main goals are to check safety and see if it can improve the eye's ability to adjust to darkness. The study involves 12 adults aged 18 to 70 with moderate to severe vision loss.