New gene therapy aims to slow vision loss in rare eye disease
NCT ID NCT05748873
First seen Nov 01, 2025 · Last updated May 08, 2026 · Updated 32 times
Summary
This study tests a one-time gene therapy injection into the eye for people with advanced retinitis pigmentosa caused by mutations in the RHO, PDE6A, or PDE6B genes. The goal is to see if it is safe and can slow vision loss. About 33 adults will take part, and the study will follow them for up to 5 years.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Bascom Palmer Eye Institute/University of Miami
RECRUITINGMiami, Florida, 33136, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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CHNO XV-XX Paris - CIC 1423
RECRUITINGParis, 75012, France
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Casey Eye Institute
RECRUITINGPortland, Oregon, 97239, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Mass Eye and Ear
RECRUITINGBoston, Massachusetts, 02114, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Retina Foundation of the Southwest
RECRUITINGDallas, Texas, 75231, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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UPMC Eye Center
RECRUITINGPittsburgh, Pennsylvania, 15213, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.