Experimental gene therapy aims to halt vision loss in rare blindness

NCT ID NCT03328130

First seen Jun 27, 2026 ยท Last updated Jun 27, 2026

Summary

This study tested a gene therapy for retinitis pigmentosa, an inherited eye disease that causes gradual vision loss. The treatment involved injecting a corrected gene under the retina in one eye. The trial included 19 people aged 13 and older with a specific genetic defect. The main goal was to check safety and see if vision improved.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary โ€” we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Eye Diseases, Hereditary eye disorder inherited retinal dystrophy retinal degeneration retinal disorder retinitis pigmentosa retinitis pigmentosa 40 vision disorder

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Clinique Ophtalmologique, CHU de Nantes

    Nantes, 44093, France