Could a single gene therapy fix hemophilia a?
NCT ID NCT03217032
First seen May 10, 2026 · Last updated May 23, 2026 · Updated 2 times
Summary
This early-phase study tests a gene therapy for hemophilia A, a bleeding disorder. Researchers take a patient's own stem cells, add a working gene for clotting factor VIII, and infuse them back. The goal is to see if this is safe and can reduce bleeding episodes. The trial involves 10 males aged 2 and older with severe hemophilia A.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Shenzhen Geno-immune Medical Institute
RECRUITINGShenzhen, Guangdong, 518000, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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