Gene therapy breakthrough for rare fabry disease?
NCT ID NCT06539624
First seen Feb 28, 2026 · Last updated May 15, 2026 · Updated 11 times
Summary
This study tests a new gene therapy, EXG110, for people with Fabry disease, a rare genetic condition. The goal is to see if it is safe and can help control the disease. About 12 people aged 7 and older will receive a single dose of the therapy. Researchers will monitor side effects and check for improvements in kidney, heart, and skin symptoms.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Children's Hospital, Zhejiang University School of Medicine
RECRUITINGHangzhou, Zhejiang, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Shanghai Children's Medical Center
RECRUITINGShanghai, Shanghai Municipality, China
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Conditions
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