Hope for rare bone disease: experimental drug garetosmab enters final testing phase

NCT ID NCT05394116

First seen Jan 17, 2026 · Last updated May 21, 2026 · Updated 18 times

Summary

This study tests an experimental drug called garetosmab in 63 adults with fibrodysplasia ossificans progressiva (FOP), a rare genetic condition where soft tissues turn into bone. The goal is to see if the drug safely reduces new abnormal bone growth and flare-ups. Participants receive either garetosmab or a placebo, and researchers monitor side effects and drug levels in the blood.

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Contacts and locations

Locations

  • Amsterdam University Medical Center

    Amsterdam, North Holland, 1081 HV, Netherlands

  • Clinica Universidad de La Sabana

    Chía, Cundinamarca, 140013, Colombia

  • HUS Children and Adolescents Park Hospital Clinical Trial Unit

    Helsinki, Stenbäckinkatu 11, 00029, Finland

  • Hopital Lariboisiere

    Paris, 75010, France

  • Hospital Israelita Albert Einstein

    São Paulo, 05652-900, Brazil

  • Hospital Kuala Lampur

    Kuala Lumpur, 50586, Malaysia

  • Hospital Universitario Ramon y Cajal

    Madrid, 28034, Spain

  • Hôpital Lapeyronie

    Montpellier, 34090, France

  • IRCCS Istituto Giannina Gaslini

    Genoa, 16147, Italy

  • Kyushu University Hospital

    Fukuoka, 812-8582, Japan

  • Nagoya University Hospital

    Nagoya, Aichi-ken, 466-8560, Japan

  • Oita University Hospital

    Yufu, Oita Prefecture, 879-5593, Japan

  • Queen Mary Hospital

    Hong Kong, 22553838, Hong Kong

  • Royal National Orthropaedic Hospital NHS Trust

    Middlesex, Greater London, HA7 4LP, United Kingdom

  • Royal North Shore Hospital

    St Leonards, New South Wales, 2065, Australia

  • Seoul National University Hospital

    Seoul, 03080, South Korea

  • Szpital Centrum Medyczne Medyk

    Rzeszów, Podkarpackie Voivodeship, 35-326, Poland

  • Tongji Hospital of Tongji University

    Shanghai, 200065, China

  • Universidad de Concepcion

    Concepción, Biobio, 4030000, Chile

  • University of California Los Angeles (UCLA) Medical Center

    Los Angeles, California, 90095, United States

  • University of Cape Town

    Rondebosch, Cape Town, 7700, South Africa

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

Conditions

Explore the condition pages connected to this study.