Terminated trial tests First-of-its-Kind treatment for kids with rare nerve disease

NCT ID NCT06681766

Summary

This study aimed to test the safety of a new drug called nomlabofusp in children and teenagers with Friedreich's ataxia, a rare genetic disorder that damages the nervous system. The trial was small, involving about 18 participants, and was designed to see how their bodies handled the drug when given as a daily injection for one week. It was an early-stage study that has since been terminated.

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Contacts and locations

Locations

  • Uncommon Cures

    Chevy Chase, Maryland, 20815, United States

Conditions

Explore the condition pages connected to this study.