New hope for kids with hemophilia: trial tests Long-Term bleeding prevention

NCT ID NCT07285460

Summary

This study is testing a drug called fitusiran to see if it can safely and effectively prevent bleeding episodes in young boys with severe hemophilia A or B. About 85 boys aged 1 to under 12 will receive the drug for up to 3 years. The main goal is to see if fitusiran reduces the number of bleeds that need treatment compared to their current standard care.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 0760004

    RECRUITING

    São Paulo, 05403-000, Brazil

  • Investigational Site Number : 0560002

    RECRUITING

    Brussels, 1020, Belgium

  • Investigational Site Number : 1240003

    RECRUITING

    Montreal, Quebec, H3T 1C5, Canada

  • Investigational Site Number : 3560001

    RECRUITING

    Pune, 411004, India

  • Investigational Site Number : 3560002

    RECRUITING

    Mumbai, 400022, India

  • Investigational Site Number : 6160002

    RECRUITING

    Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

  • Investigational Site Number : 7240001

    RECRUITING

    Esplugues de Llobregat, Barcelona [Barcelona], 08950, Spain

  • Investigational Site Number : 7240002

    RECRUITING

    Madrid, 28046, Spain

  • Investigational Site Number : 7240003

    RECRUITING

    Zaragoza, 50009, Spain

  • Investigational Site Number : 7920001

    RECRUITING

    Istanbul, 34093, Turkey (Türkiye)

  • Investigational Site Number : 7920002

    RECRUITING

    Izmir, 35100, Turkey (Türkiye)

  • The Center for Inherited Blood Disorders- Site Number : 8400009

    RECRUITING

    Orange, California, 92868, United States

  • The Luskin Orthopaedic Institute for Children- Site Number : 8400013

    RECRUITING

    Los Angeles, California, 90007, United States

Conditions

Explore the condition pages connected to this study.