New shot could help young boys with hemophilia avoid bleeding episodes
NCT ID NCT07285460
First seen Jan 10, 2026 · Last updated May 15, 2026 · Updated 19 times
Summary
This study tests a medicine called fitusiran in boys aged 1 to under 12 with severe hemophilia A or B, including those whose bodies have developed antibodies that block standard treatments. The goal is to see if regular shots of fitusiran can reduce the number of bleeding episodes. About 85 boys will take part, some switching from their usual care and others joining directly.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Cure 4 The Kids Foundation- Site Number : 8400001
RECRUITINGLas Vegas, Nevada, 89147, United States
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Hackensack Meridian Health - Hackensack University Medical Center- Site Number : 8400008
RECRUITINGHackensack, New Jersey, 07601, United States
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Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 0760004
RECRUITINGSão Paulo, 05403-000, Brazil
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Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 0760003
RECRUITINGRibeirão Preto, São Paulo, 14051140, Brazil
Contact Phone: •••-•••-••••
Contact
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Investigational Site Number : 0560001
RECRUITINGBrussels, 1200, Belgium
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Investigational Site Number : 0560002
RECRUITINGBrussels, 1020, Belgium
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Investigational Site Number : 1240003
RECRUITINGMontreal, Quebec, H3T 1C5, Canada
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Investigational Site Number : 1580001
RECRUITINGTaipei, 100, Taiwan
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Investigational Site Number : 1580002
RECRUITINGTaichung, 402, Taiwan
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Investigational Site Number : 3560001
RECRUITINGPune, 411004, India
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Investigational Site Number : 3560002
RECRUITINGMumbai, 400022, India
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Investigational Site Number : 3800001
RECRUITINGMilan, Milano, 20122, Italy
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Investigational Site Number : 3800002
RECRUITINGFlorence, Firenze, 50134, Italy
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Investigational Site Number : 3800003
RECRUITINGRozzano, Milano, 20089, Italy
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
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Investigational Site Number : 6160002
RECRUITINGWroclaw, Lower Silesian Voivodeship, 50-556, Poland
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Investigational Site Number : 6420001
RECRUITINGIași, 700309, Romania
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Investigational Site Number : 6420003
RECRUITINGTimișoara, 300011, Romania
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Investigational Site Number : 7240001
RECRUITINGEsplugues de Llobregat, Barcelona [Barcelona], 08950, Spain
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Investigational Site Number : 7240002
RECRUITINGMadrid, 28046, Spain
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Investigational Site Number : 7240003
RECRUITINGZaragoza, 50009, Spain
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Investigational Site Number : 7920001
RECRUITINGIstanbul, 34093, Turkey (Türkiye)
Contact
Contact Phone: •••-•••-••••
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Investigational Site Number : 7920002
RECRUITINGIzmir, 35100, Turkey (Türkiye)
Contact Phone: •••-•••-••••
Contact
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The Center for Inherited Blood Disorders- Site Number : 8400009
RECRUITINGOrange, California, 92868, United States
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The Luskin Orthopaedic Institute for Children- Site Number : 8400013
RECRUITINGLos Angeles, California, 90007, United States
Conditions
Explore the condition pages connected to this study.