Extended hope for rare blood fat disorder
NCT ID NCT05130450
Summary
This study provides continued access to the experimental drug olezarsen for up to 60 patients with Familial Chylomicronemia Syndrome (FCS), a rare genetic disorder causing extremely high blood fats. The main goal is to gather long-term safety data and see if the drug keeps lowering dangerous triglyceride levels over three years of treatment. Participants are those who successfully completed the previous trial and will receive injections for about 157 weeks.
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Contacts and locations
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Locations
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Academisch Medisch Centrum Goederenontvangst Apotheek t.a.v. Kenniscentrum
Amsterdam, Noor-Holland, 1105 AZ, Netherlands
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Apokteket AB
Malmo, 211 24, Sweden
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Azienda Ospedaliero Universitaria Policlinico Umberto I
Rome, 00161, Italy
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CTSI Investigational Pharmacy
New York, New York, 10016, United States
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Clinique des Maladies Lipidiques de Quebec Inc.
Québec, Quebec, G1V 4W2, Canada
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Department of Pharmacy
Park Ridge, Illinois, 60068, United States
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Diabetes/Lipid Management & Research Center
Huntington Beach, California, 92648, United States
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Dra Margarida Falcao Centro Hospitalar Lisboa Ocidental Hospital Egas Moniz
Lisbon, 1340-019, Portugal
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Ecogene-21
Chicoutimi, Quebec, G7H 7K9, Canada
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Excel Medical Clinical Trials, LLC
Boca Raton, Florida, 33434, United States
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Groupement Hospitalier Est- Pharmacie Secteur Essais Clinique
Bron, 69677, France
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Hospital Clínic Barcelona C/ Villarroel
Barcelona, 08036, Spain
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Hospital Universitario 12 de Octubre
Madrid, 28041, Spain
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Hospital Universitario Virgen del Rocío
Seville, 41013, Spain
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Hospital da Senhora da Oliveira Guimaraes
Creixomil, 4835-044, Portugal
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Hôpital Bicêtre
Le Kremlin-Bicêtre, 94270, France
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IDS Central
Philadelphia, Pennsylvania, 19104, United States
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Institute de Recherches Cliniques de Montreal
Montreal, Quebec, H2W 1R7, Canada
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Metabolicke centrum MU
Bratislava, 83101, Slovakia
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Milstein Hospital
New York, New York, 10032, United States
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Nathalie Saint-Pierre
Montreal, Quebec, H2W 1R7, Canada
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Oslo Hospital Pharmacy Rikshospitalet
Oslo, 0372, Norway
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Pharmacie Hopital de la Conception
Marseille, 05 13385, France
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Royal Manchester Children's Hospital
Manchester, M13 9WL, United Kingdom
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UOC di Farmacia AOUP PAOLO GIACCONE
Palermo, 90127, Italy
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University of Kansas Medical Center (KUMC)
Kansas City, Kansas, 66160, United States
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Via Sergio Pansini 5
Naples, 80131, Italy
Conditions
Explore the condition pages connected to this study.