FAMILIAL CHYLOMICRONEMIA SYNDROME
Clinical trials for FAMILIAL CHYLOMICRONEMIA SYNDROME explained in plain language.
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New drug tested for rare, painful fat disorder
Disease control OngoingThis study is checking the long-term safety of an experimental drug called olezarsen for people with Familial Chylomicronemia Syndrome (FCS), a rare genetic disorder that causes extremely high fat levels in the blood and painful pancreas attacks. It is for 24 people who have alre…
Matched conditions: FAMILIAL CHYLOMICRONEMIA SYNDROME
Phase: PHASE3 • Sponsor: Ionis Pharmaceuticals, Inc. • Aim: Disease control
Last updated Apr 02, 2026 05:41 UTC
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Extended hope for rare blood fat disorder
Disease control OngoingThis study provides continued access to the experimental drug olezarsen for up to 60 patients with Familial Chylomicronemia Syndrome (FCS), a rare genetic disorder causing extremely high blood fats. The main goal is to gather long-term safety data and see if the drug keeps loweri…
Matched conditions: FAMILIAL CHYLOMICRONEMIA SYNDROME
Phase: PHASE3 • Sponsor: Ionis Pharmaceuticals, Inc. • Aim: Disease control
Last updated Mar 31, 2026 12:12 UTC
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New shot aims to tame dangerous blood fats
Disease control OngoingThis early-stage study is testing a new drug called RN0361 to see if it is safe and can lower very high levels of triglycerides (a type of fat) in the blood. It will involve about 108 healthy adults and adults with high triglycerides. The main goals are to check for side effects …
Matched conditions: FAMILIAL CHYLOMICRONEMIA SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: Ikaria Bioscience Pty Ltd • Aim: Disease control
Last updated Mar 27, 2026 12:39 UTC