Tracking a rare disease treatment: can enzyme therapy protect vital organs?

NCT ID NCT07187440

Summary

This study aims to understand how well a manufactured enzyme therapy works for people in China living with Fabry disease, a rare inherited disorder. Researchers will observe 200 children and adults who are already receiving this standard treatment in their regular care. The main goal is to see how the treatment affects their heart and kidney function over time in real-world settings.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Affiliated Drum Tower Hospital, Medical School of Nanjing University

    RECRUITING

    Nanjing, Jiangsu, 210008, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Fuzhou University Provincial Affiliated Hospital

    RECRUITING

    Fuzhou, Fujian, 350001, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Peking Union Medical College Hospital

    RECRUITING

    Beijing, Beijing Municipality, 100730, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Peking University First Hospital

    NOT_YET_RECRUITING

    Beijing, Beijing Municipality, 100034, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Peking University Third Hospital

    RECRUITING

    Beijing, Beijing Municipality, 100191, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Second Hospital Of ShanXi Medical University

    NOT_YET_RECRUITING

    Taiyuan, Shanxi, '030001, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • ShanTou Central Hospital

    RECRUITING

    Shantou, Guangdong, 515031, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The First Affiliated Hospital Of Soochow University

    RECRUITING

    Suzhou, Jiangsu, 215006, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The First Affiliated Hospital Of USTC (AnHui Provincial Hospital)

    NOT_YET_RECRUITING

    Hefei, Anhui, 230001, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The First Affiliated Hospital With NanJing Medical University(JiangSu Province Hospital)

    NOT_YET_RECRUITING

    Nanjing, Jiangsu, 210029, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The First Affiliated Hospital of Xi 'an Jiaotong University

    NOT_YET_RECRUITING

    Xi'an, Shaanxi, 710061, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Affiliated Hospital ZheJiang University School Of Medicine

    NOT_YET_RECRUITING

    Hangzhou, Guangdong, 310009, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Affiliated Hospital of Harbin Medical University

    NOT_YET_RECRUITING

    Harbin, Heilongjiang, 150086, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The Second Affiliated Hospital of Xi 'an Jiaotong University

    RECRUITING

    Xi'an, Shaanxi, 710004, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Hospital of Hebei Medical University

    RECRUITING

    Shijiazhuang, Hebei, '050000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The University Of Hong Kong-ShenZhen Hospital

    NOT_YET_RECRUITING

    Shenzhen, Guangdong, 518053, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • TianJin Chest Hospital

    NOT_YET_RECRUITING

    Tianjin, Tianjin Municipality, 300222, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • West China Hospital of Sichuan University

    NOT_YET_RECRUITING

    Chengdu, Sichuan, 610041, China

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.