Researchers track fabry patients to see how treatments work over time
NCT ID NCT06906367
First seen Nov 01, 2025 · Last updated May 05, 2026 · Updated 28 times
Summary
This study follows 450 adults with Fabry disease to see how well treatments, especially migalastat, work over the long term. Researchers will measure kidney function, track heart and brain events, and check quality of life. Participants are either already taking migalastat or starting it, and the study does not involve any experimental drugs.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Arkansas Children's Hospital
RECRUITINGLittle Rock, Arkansas, 72202, United States
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Emory Genetics
RECRUITINGAtlanta, Georgia, 30322, United States
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Lysosomal and Rare Disorders Research and Treatment Center, Inc.
RECRUITINGFairfax, Virginia, 22030, United States
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New York-Presbyterian Morgan Stanley Children's Hospital - Columbia University Medical Center
NOT_YET_RECRUITINGNew York, New York, 10032, United States
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Renal Disease Research Institute
RECRUITINGDallas, Texas, 75204, United States
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UAB Nephrology Research Clinic at Paula Building
NOT_YET_RECRUITINGBirmingham, Alabama, 35233, United States
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UPMC Children's Hospital of Pittsburgh
NOT_YET_RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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Washington University School of Medicine
NOT_YET_RECRUITINGSt Louis, Missouri, 63110, United States
Conditions
Explore the condition pages connected to this study.