Researchers track fabry patients to see how treatments work over time

NCT ID NCT06906367

First seen Nov 01, 2025 · Last updated May 05, 2026 · Updated 28 times

Summary

This study follows 450 adults with Fabry disease to see how well treatments, especially migalastat, work over the long term. Researchers will measure kidney function, track heart and brain events, and check quality of life. Participants are either already taking migalastat or starting it, and the study does not involve any experimental drugs.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Arkansas Children's Hospital

    RECRUITING

    Little Rock, Arkansas, 72202, United States

  • Emory Genetics

    RECRUITING

    Atlanta, Georgia, 30322, United States

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc.

    RECRUITING

    Fairfax, Virginia, 22030, United States

  • New York-Presbyterian Morgan Stanley Children's Hospital - Columbia University Medical Center

    NOT_YET_RECRUITING

    New York, New York, 10032, United States

  • Renal Disease Research Institute

    RECRUITING

    Dallas, Texas, 75204, United States

  • UAB Nephrology Research Clinic at Paula Building

    NOT_YET_RECRUITING

    Birmingham, Alabama, 35233, United States

  • UPMC Children's Hospital of Pittsburgh

    NOT_YET_RECRUITING

    Pittsburgh, Pennsylvania, 15224, United States

  • Washington University School of Medicine

    NOT_YET_RECRUITING

    St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.