Gene therapy RGX-202 made available for single patients in need

NCT ID NCT07652606

TEMPORARILY_NOT_AVAILABLE Disease control Sponsor: REGENXBIO Inc. Source: ClinicalTrials.gov ↗

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This program allows eligible patients to receive RGX-202, a gene therapy, on a single-patient basis outside of a clinical trial. It is designed for those with serious conditions who have no other treatment options. Currently, the program is temporarily not available.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

RGX-202 gene therapy

What this could lead to

If successful, this expanded access program could provide a treatment option for individual patients who have no other alternatives.

What could go wrong

This is an expanded access program, not a clinical trial, so there is limited data on safety and effectiveness. The treatment is temporarily unavailable, and results may not apply to other patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Duchenne muscular dystrophy

Contacts and locations

Locations

  • Regenxbio

    Rockville, Maryland, 20850, United States