New stem cell therapy aims to free patients from lifelong blood transfusions
NCT ID NCT04390971
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tested a new treatment called ET-01 in 3 people with transfusion-dependent beta-thalassemia, a blood disorder that requires regular blood transfusions. The treatment uses the patient's own stem cells, which are modified and then transplanted back. The goal was to see if it is safe and can reduce or eliminate the need for transfusions by helping the body produce healthy red blood cells.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Affiliated Hospital of Zunyi Medical University
Zunyi, Guizhou, 563000, China
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Institute of Hematology & Blood Diseases Hospital
Tianjin, Tianjin Municipality, 300020, China
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The Affiliated Hospital of Guizhou Medical University
Guiyang, Guizhou, 550004, China