New hope for aplastic anemia: drug combo aims to cut transfusions

NCT ID NCT07548671

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This Phase 3 trial tests whether adding enarodustat to standard cyclosporine treatment helps people with transfusion-dependent non-severe aplastic anemia. The study will enroll 90 newly diagnosed adults who cannot have a stem cell transplant. The goal is to see if the combination improves blood counts and reduces the need for transfusions compared to cyclosporine alone.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
enarodustat and cyclosporine
What this could lead to
If successful, this combination could become a new standard treatment for transfusion-dependent non-severe aplastic anemia, reducing or eliminating the need for blood transfusions.
What could go wrong
This is a Phase 3 trial, but it has not yet started recruiting. The combination may not be more effective than cyclosporine alone, and both drugs carry risks like kidney problems or infections.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

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Contacts and locations

Study contacts

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