Doctors track new hemophilia drug in babies under 3

NCT ID NCT05248594

Summary

This study collected real-world information about how doctors use the medication emicizumab to prevent bleeding in very young children (ages 0-3) with hemophilia A. Researchers reviewed medical records from 71 children across several treatment centers to understand common dosing practices, how well the drug prevented bleeding, and how surgeries were managed while on the medication. The goal was to gather practical experience to help guide treatment for other young children.

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Contacts and locations

Locations

  • Children's Hospital at Montefiore

    The Bronx, New York, 10467, United States

  • Comprehensive Center for Hemophilia and Coagulation Disorders (Cornell)

    New York, New York, 10065, United States

  • Connecticut Children's Hemophilia Treatment Center - Connecticut Children's Medical Center

    Hartford, Connecticut, 06106, United States

  • Dartmouth Hitchcock Hemophilia Center - Mary Hitchcock Memorial Hospital

    Lebanon, New Hampshire, 03766, United States

  • Mary M Gooley Hemophilia Center, Inc.

    Rochester, New York, 14621, United States

  • Newark Beth Israel

    Newark, New Jersey, 07112, United States

  • Northwell Health Hemostasis and Thrombosis Center

    Staten Island, New York, 11030, United States

  • SUNY Upstate Hemophilia Treatment Center - HTC 058

    Syracuse, New York, 13210, United States

  • Western NY Blood Care - Research Foundation for SUNY

    Buffalo, New York, 14202, United States

  • Yale Hemophilia Treatment Center

    New Haven, Connecticut, 06510, United States

Conditions

Explore the condition pages connected to this study.