New hope for rare disease patients with severe gut problems

NCT ID NCT07202598

Summary

This study is testing if a drug called emapalumab can help control severe intestinal inflammation in people with APECED, a rare autoimmune disease. Up to 10 participants, aged 2 to 75, will receive the drug through an IV over several months. The main goal is to see if it safely reduces gut symptoms and improves quality of life.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.