New drug combo shows promise for rare blood disorder

NCT ID NCT01623167

First seen Apr 23, 2026 · Last updated May 03, 2026 · Updated 2 times

Summary

This study tests whether adding eltrombopag to standard immune-suppressing drugs can help people with severe aplastic anemia, a rare condition where the immune system attacks the bone marrow. About 207 untreated patients aged 2 and older will receive the combination and be monitored for improved blood cell counts. The goal is to see if this approach is safe and more effective than standard treatment alone.

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Contacts and locations

Locations

  • National Institutes of Health Clinical Center, 9000 Rockville Pike

    Bethesda, Maryland, 20892, United States

Conditions

Explore the condition pages connected to this study.