New drug trial targets debilitating muscle disease

NCT ID NCT05481879

Summary

This study is testing an investigational drug called DYNE-101 for adults with myotonic dystrophy type 1 (DM1), a genetic disorder that causes progressive muscle weakness and stiffness. The main goals are to see if the drug is safe and if it can improve muscle function and reduce stiffness. Participants will receive the drug or a placebo via IV infusion over several months while researchers measure changes in their symptoms and physical abilities.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for MYOTONIC DYSTROPHY TYPE 1 (DM1) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CHU de Nantes

    RECRUITING

    Nantes, 44093, France

    Contact Email: •••••@•••••

    Contact

  • Centro Clinico Nemo

    RECRUITING

    Milan, 20162, Italy

    Contact Email: •••••@•••••

    Contact

  • Charité - Universitätsmedizin Berlin

    RECRUITING

    Berlin, 10117, Germany

    Contact

    Contact Email: •••••@•••••

  • Fondazione Policlinico Universitario A Gemelli-Rome

    RECRUITING

    Rome, 00168, Italy

    Contact Email: •••••@•••••

    Contact

  • Indiana University School of Medicine

    RECRUITING

    Indianapolis, Indiana, 46202, United States

    Contact

    Contact Email: •••••@•••••

  • Institut de Myologie

    RECRUITING

    Paris, 75013, France

    Contact Email: •••••@•••••

    Contact

  • John Walton Muscular Dystrophy Research Centre

    RECRUITING

    Newcastle upon Tyne, United Kingdom

    Contact

    Contact Email: •••••@•••••

  • Ludwig Maximilians University, Munich - Friedrich Baur Institut

    RECRUITING

    Munich, 80336, Germany

    Contact

    Contact Email: •••••@•••••

    Contact

  • NZCR Auckland

    RECRUITING

    Auckland, 1023, New Zealand

    Contact

    Contact Email: •••••@•••••

  • Neurology Rare Disease Center

    RECRUITING

    Denton, Texas, 76208, United States

    Contact

    Contact Email: •••••@•••••

  • Radboud Medical Center

    RECRUITING

    Nijmegen, Netherlands

    Contact Email: •••••@•••••

    Contact

  • Salford Royal Hospital

    RECRUITING

    Salford, M6 8HD, United Kingdom

    Contact Email: •••••@•••••

    Contact

  • St. Vincent's Hospital

    RECRUITING

    Fitzroy, Victoria, 3065, Australia

    Contact Email: •••••@•••••

    Contact

  • University College London Hospitals

    RECRUITING

    London, NW1 2BU, United Kingdom

    Contact

    Contact Email: •••••@•••••

  • University of Iowa

    RECRUITING

    Iowa City, Iowa, 52242, United States

    Contact

    Contact Email: •••••@•••••

  • University of Rochester Medical Center

    RECRUITING

    Rochester, New York, 14642, United States

    Contact

    Contact Email: •••••@•••••

  • Virginia Commonwealth University (VCU)

    RECRUITING

    Richmond, Virginia, 23298, United States

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.