FDA-Approved drug tested to restore vision in genetic color blindness

NCT ID NCT04041232

Summary

This early-stage study is testing whether an existing drug called glycerol phenylbutyrate (PBA) can improve vision in people with a rare, inherited form of color blindness caused by a specific gene mutation (ATF6). Two adult patients will take the drug three times a day and have their vision and eye health closely monitored over several clinic visits. The goal is to see if PBA can reduce cellular stress in the eye and improve retinal function.

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Contacts and locations

Locations

  • Columbia University Irving Medical Center

    New York, New York, 10032, United States

Conditions

Explore the condition pages connected to this study.